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1 . Academic Journal
Association of busulfan exposure with survival and toxicity after haemopoietic cell transplantation in children and young adults: a multicentre, retrospective cohort analysis
저자
by
Bartelink, Imke H
;
Lalmohamed, Arief
;
van Reij, Elisabeth M L
;
Dvorak, Christopher C
;
Savic, Rada M
, et al.
소스
In
The Lancet Haematology
November 2016 3(11):e526-e536
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7 . Academic Journal
Dual Antigen Targeting with Co-Transduced CD19/22 CAR T Cells May Prevent Antigen-Negative Relapse after CAR T Cell Therapy for Relapsed/Refractory ALL
저자
by
Ghorashian, Sara
;
Lucchini, Giovanna
;
Richardson, Rachel
;
Nguyen, Kyvi
;
Terris, Craig
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:10352-10354
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7 . Academic Journal
Systematic Intention to Treat Analysis of Real-World Outcomes in Children and Young Adults Receiving Tisagenlecleucel: From Elegibility through Treatment Failure
저자
by
Oporto Espuelas, Macarena
;
Burridge, Saskia
;
Bonney, Denise
;
Watts, Kelly
;
Roddie, Claire
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:2408-2410
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7 . Academic Journal
Specific Cytogenetic Abnormalities at Diagnosis Predict Survival after Hematopoietic Cell Transplant in Poor-Risk Pediatric Acute Myeloid Leukemia: A PDWP/EBMT Study
저자
by
Sharma, Akshay
;
Galimard, Jacques-Emmanuel
;
Pryce, Angharad
;
Bhoopalan, Senthil
;
Dalissier, Arnaud
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:1882-1884
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7 . Academic Journal
Outcome of Haematopoietic Cell Transplantation in 813 Children with Fanconi Anaemia: A Study on Behalf of the EBMT Severe Aplastic Anaemia Working Party and Paediatric Disease Working Party
저자
by
Lum, Su Han
;
Samarasinghe, Sujith
;
Eikema, Dirk-Jan
;
Piepenbroek, Brian
;
Dalissier, Arnaud
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:657-659
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7 . Academic Journal
Design of a Multi-Center Randomized Active Controlled Phase 3 Clinical Trial (HURCULES) Evaluating the Safety and Efficacy of OTL-203 in Patients with MPS-IH Versus Standard of Care with Allogeneic Hematopoietic Stem Cell Transplantation
저자
by
Gupta, Ashish O.
;
Wynn, Robert F
;
Kharbanda, Sandhya
;
Lindemans, Caroline A.
;
Ahrens-Nicklas, Rebecca
, et al.
소스
In
Transplantation and Cellular Therapy
February 2024 30(2) Supplement:S236-S237
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7 . Academic Journal
Survey of Infection Surveillance, Prophylaxis, and Vaccination Practices after Autologous Genetically Modified Cellular Therapies
저자
by
John, Tami
;
Marón, Gabriela M.
;
Abraham, Allistair
;
Bertaina, Alice
;
Bhoopalan, Senthil Velan
, et al.
소스
In
Transplantation and Cellular Therapy
February 2024 30(2) Supplement:S235-S235
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7 . Academic Journal
Preliminary Results of a Phase 2a Clinical Trial to Evaluate Safety, Tolerability and Antiviral Activity of Intravenous Brincidofovir (BCV IV) in Immunocompromised Patients with Adenovirus Infection
저자
by
Grimley, Michael
;
Marón, Gabriela M.
;
Gomez, Carlos A
;
Prasad, Vinod K
;
Dara, Jasmeen
, et al.
소스
In
Transplantation and Cellular Therapy
February 2024 30(2) Supplement:S89-S89
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7 . Academic Journal
Transplantation for Congenital Sideroblastic Anaemia Is Feasible and Offers Outcomes Comparable to Other Transfusion Dependent Anaemias. a Joint Retrospective Study of the Paediatric Diseases and Severe Aplastic Anaemia Working Parties (PDWP/SAAWP) of EBMT
저자
by
de la Fuente, Josu
;
Eikema, Dirk-Jan
;
Bosman, Paul
;
Wynn, Robert F
;
Díaz, Miguel
, et al.
소스
In
Blood
5 November 2020 136 Supplement 1:45-47
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7 . Academic Journal
Outcomes of Allogeneic Hematopoietic Stem Cell Transplantation for Congenital Amegakaryocytic Thrombocytopenia, a PDWP/EBMT Study
저자
by
Aldebert, Clemence
;
Fahd, Mony
;
Galimard, Jacques-Emmanuel
;
Ghemlas, Ibrahim A.
;
Zecca, Marco
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:10895-10896
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