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1 . Academic Journal
Intermittent lipid nanoparticle mRNA administration prevents cortical dysmyelination associated with arginase deficiency
저자
by
Suhail Khoja
;
Xiao-Bo Liu
;
Brian Truong
;
Matthew Nitzahn
;
Jenna Lambert
, et al.
소스
Molecular Therapy: Nucleic Acids, Vol 28, Iss , Pp 859-874 (2022)
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7 . Academic Journal
Gene therapy for guanidinoacetate methyltransferase deficiency restores cerebral and myocardial creatine while resolving behavioral abnormalities
저자
by
Suhail Khoja
;
Jenna Lambert
;
Matthew Nitzahn
;
Adam Eliav
;
YuChen Zhang
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 25, Iss , Pp 278-296 (2022)
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7 . Academic Journal
CD13 and ROR2 Permit Isolation of Highly Enriched Cardiac Mesoderm from Differentiating Human Embryonic Stem Cells
저자
by
Rhys J.P. Skelton
;
Bevin Brady
;
Suhail Khoja
;
Debashis Sahoo
;
James Engel
, et al.
소스
Stem Cell Reports, Vol 6, Iss 1, Pp 95-108 (2016)
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7 . Academic Journal
Genetic analysis of HIV-1 subtypes in Nairobi, Kenya.
저자
by
Suhail Khoja
;
Peter Ojwang
;
Saeed Khan
;
Nancy Okinda
;
Reena Harania
, et al.
소스
PLoS ONE, Vol 3, Iss 9, p e3191 (2008)
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7 .
Hepatic glutamine synthetase augmentation enhances ammonia detoxification
저자
by
Leandro R. Soria
;
Gerald S. Lipshutz
;
Angela De Angelis
;
Philip Ng
;
Sergio Attanasio
, et al.
소스
J Inherit Metab Dis
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7 .
Human hepatocyte transplantation corrects the inherited metabolic liver disorder arginase deficiency in mice
저자
by
Alex K. Lam
;
Michael G. Lin
;
Stephanie A.K. Angarita
;
Suhail Khoja
;
Brian Truong
, et al.
소스
Molecular genetics and metabolism, vol 124, iss 2
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7 .
A constitutive knockout of murine carbamoyl phosphate synthetase 1 results in death with marked hyperglutaminemia and hyperammonemia
저자
by
Jenna R Lambert
;
Gerald S. Lipshutz
;
Johannes Häberle
;
Brian Truong
;
Matthew Nitzahn
, et al.
소스
J Inherit Metab Dis
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7 .
Split AAV-Mediated Gene Therapy Restores Ureagenesis in a Murine Model of Carbamoyl Phosphate Synthetase 1 Deficiency
저자
by
Gabriella Allegri
;
Matthew Nitzahn
;
Suhail Khoja
;
Georgios Makris
;
Gerald S. Lipshutz
, et al.
소스
Mol Ther
Molecular therapy : the journal of the American Society of Gene Therapy, vol 28, iss 7
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7 .
Noncoding Centromeric RNA Expression Impairs Chromosome Stability in Human and Murine Stem Cells
저자
by
Zoia L. Monaco
;
Suhail Khoja
;
Daniela Moralli
;
David Yiu Leung Chan
.
소스
Disease Markers
Disease Markers, Vol 2017 (2017)
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Scopus
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6 .
CD13 and ROR2 Permit Isolation of Highly Enriched Cardiac Mesoderm from Differentiating Human Embryonic Stem Cells
저자
by
Edouard G. Stanley
;
Oscar J. Abilez
;
Rhys J.P. Skelton
;
David A. Elliott
;
Murray Kwon
, et al.
소스
Skelton, RJP; Brady, B; Khoja, S; Sahoo, D; Engel, J; Arasaratnam, D; et al.(2016). CD13 and ROR2 Permit Isolation of Highly Enriched Cardiac Mesoderm from Differentiating Human Embryonic Stem Cells. Stem Cell Reports, 6(1), 95-108. doi: 10.1016/j.stemcr.2015.11.006. UCLA: Retrieved from: http://www.escholarship.org/uc/item/3h0177zq
Stem cell reports, vol 6, iss 1
Stem Cell Reports, Vol 6, Iss 1, Pp 95-108 (2016)
Stem Cell Reports
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