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1 . Academic Journal
Innovations in RNA therapy for hemophilia
저자
by
Ragni, Margaret V.
;
Chan, Stephen Y.
.
소스
In
Blood
9 November 2023 142(19):1613-1621
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4 . Academic Journal
A review of the rationale for gene therapy for hemophilia A with inhibitors: one-shot tolerance and treatment?
저자
by
Valentino, Leonard A.
;
Ozelo, Margareth C.
;
Herzog, Roland W.
;
Key, Nigel S.
;
Pishko, Allyson M.
, et al.
소스
In
Journal of Thrombosis and Haemostasis
November 2023 21(11):3033-3044
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7 . Academic Journal
Long-term outcomes of prophylaxis with a recombinant factor VIII Fc or recombinant factor IX Fc in patients with hemophilia previously treated on demand
저자
by
Álvarez-Román, María-Teresa
;
Shapiro, Amy D.
;
Ragni, Margaret V.
;
Palmborg, Helena
;
Bystrická, Linda
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
August 2023 7(6)
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7 . Academic Journal
Prophylaxis with a recombinant factor VIII Fc in hemophilia A: long-term follow-up on joint health, efficacy, and safety from phase 3 studies in children and adults
저자
by
Konkle, Barbara A.
;
Oldenburg, Johannes
;
Pasi, John
;
Kulkarni, Roshni
;
Nolan, Beatrice
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
August 2023 7(6)
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7 . Academic Journal
Post hoc longitudinal assessment of the efficacy and safety of recombinant factor IX Fc fusion protein in hemophilia B
저자
by
Shapiro, Amy D.
;
Kulkarni, Roshni
;
Ragni, Margaret V.
;
Chambost, Hervé
;
Mahlangu, Johnny
, et al.
소스
In
Blood Advances
11 July 2023 7(13):3049-3057
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7 . Academic Journal
Prevalence and risk factors for bleeding in hereditary hemorrhagic telangiectasia: a National Inpatient Sample study
저자
by
Zarka, Jabra
;
Jeong, Kwonho
;
Yabes, Jonathan G.
;
Ragni, Margaret V.
.
소스
In
Blood Advances
July 2023
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6 . Academic Journal
Managing surgery in hemophilia with recombinant factor VIII Fc and factor IX Fc: Data on safety and effectiveness from phase 3 pivotal studies
저자
by
Chowdary, Pratima
;
Holmström, Margareta
;
Mahlangu, Johnny N.
;
Ozelo, Margaret C.
;
Pabinger, Ingrid
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
July 2022 6(5)
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7 . Academic Journal
Defenestrated endothelium delays liver-directed gene transfer in hemophilia A mice
저자
by
Kaminski, Tomasz W.
;
Ju, Eun-Mi
;
Gudapati, Shweta
;
Vats, Ravi
;
Arshad, Sanya
, et al.
소스
In
Blood Advances
28 June 2022 6(12):3729-3734
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7 . Academic Journal
Postoperative bleeding complications in patients with hemophilia undergoing major orthopedic surgery: A prospective multicenter observational study
저자
by
Kleiboer, Brendan
;
Layer, Marcus A.
;
Cafuir, Lorraine A.
;
Cuker, Adam
;
Escobar, Miguel
, et al.
소스
In
Journal of Thrombosis and Haemostasis
April 2022 20(4):857-865
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7 . Academic Journal
Whole-exome analysis of adolescents with low VWF and heavy menstrual bleeding identifies novel genetic associations
저자
by
Sadler, Brooke
;
Minard, Charles G.
;
Haller, Gabe
;
Gurnett, Christina A.
;
O'Brien, Sarah H.
, et al.
소스
In
Blood Advances
25 January 2022 6(2):420-428
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