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1 . Academic Journal
Prevention of early-onset cardiomyopathy in Dmd exon 52–54 deletion mice by CRISPR-Cas9-mediated exon skipping
저자
by
Rok, Matthew
;
Ying Wong, Tatianna Wai
;
Maino, Eleonora
;
Ahmed, Abdalla
;
Yang, Grace
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
July 2023
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7 . Academic Journal
Targeted genome editing in vivo corrects a Dmd duplication restoring wild‐type dystrophin expression.
저자
by
Maino, Eleonora
;
Wojtal, Daria
;
Evagelou, Sonia L
;
Farheen, Aiman
;
Wong, Tatianna W Y
, et al.
소스
EMBO Molecular Medicine; 5/7/2021, Vol. 13 Issue 5, p1-15, 15p
Open Access (Wiley)
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7 . Academic Journal
A mutation-independent approach for muscular dystrophy via upregulation of a modifier gene.
저자
by
Kemaladewi, Dwi U.
;
Bassi, Prabhpreet S.
;
Erwood, Steven
;
Al-Basha, Dhekra
;
Gawlik, Kinga I.
, et al.
소스
Nature; 8/1/2019, Vol. 572 Issue 7767, p125-130, 6p, 8 Color Photographs, 2 Black and White Photographs, 1 Diagram, 2 Graphs
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7 . Academic Journal
A novel mouse model of Duchenne muscular dystrophy carrying a multi-exonic Dmd deletion exhibits progressive muscular dystrophy and early-onset cardiomyopathy
저자
by
Wong, Tatianna Wai Ying
;
Ahmed, Abdalla
;
Yang, Grace
;
Maino, Eleonora
;
Steiman, Sydney
, et al.
소스
DISEASE MODELS & MECHANISMS
; SEP 2020, 13 9, pdmm045369 12p.
Scopus
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7 . Academic Journal
Spell Checking Nature: Versatility of CRISPR/Cas9 for Developing Treatments for Inherited Disorders.
저자
by
Wojtal, Daria
;
Kemaladewi, Dwi U.
;
Malam, Zeenat
;
Abdullah, Sarah
;
Wong, Tatianna W. Y.
, et al.
소스
American Journal of Human Genetics
. Jan2016, Vol. 98 Issue 1, p90-101. 12p.
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7 . Academic Journal
Cell Surface Profiling Using High-Throughput Flow Cytometry: A Platform for Biomarker Discovery and Analysis of Cellular Heterogeneity.
저자
by
Gedye, Craig A.
;
Hussain, Ali
;
Paterson, Joshua
;
Smrke, Alannah
;
Saini, Harleen
, et al.
소스
PLoS ONE
. Aug2014, Vol. 9 Issue 8, p1-14. 14p.
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7 . Academic Journal
Patient-Derived Xenografts for Prognostication and Personalized Treatment for Head and Neck Squamous Cell Carcinoma
저자
by
Karamboulas, Christina
;
Bruce, Jeffrey P.
;
Hope, Andrew J.
;
Meens, Jalna
;
Huang, Shao Hui
, et al.
소스
CELL REPORTS
; OCT 30 2018, 25 5, p1318-p+, 18p.
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7 . Periodical
Correction of a splicing defect in a mouse model of congenital muscular dystrophy type 1A using a homology-directed-repair-independent mechanism
저자
by
Kemaladewi, Dwi U
;
Maino, Eleonora
;
Hyatt, Elzbieta
;
Hou, Huayun
;
Ding, Maylynn
, et al.
소스
Nature Medicine; August 2017, Vol. 23 Issue: 8 p984-989, 6p
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7 . Academic Journal
Improved Electrospray Ionization Efficiency Compensates for Diminished Chromatographic Resolution and Enables Proteomics Analysis of Tyrosine Signaling in Embryonic Stem Cells.
저자
by
Ficarro, Scott B.
;
Yi Zhang
;
Yu Lu
;
Moghimi, Ahmadali R.
;
Askenazi, Manor
, et al.
소스
Analytical Chemistry
. 5/1/2009, Vol. 81 Issue 9, p3440-3447. 8p.
Full Text (ACS)
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7 . Book
The K/BxN Mouse Model of Inflammatory Arthritis.
저자
by
Walker, John M.
;
Cope, Andrew P.
;
Monach, Paul
;
Hattori, Kimie
;
Huang, Haochu
, et al.
소스
Arthritis Research (9781588299185); 2007, p269-282, 14p
Find it @ DONGA
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