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1 . Academic Journal
Performing and interpreting individual pharmacokinetic profiles in patients with Hemophilia A or B: Rationale and general considerations
저자
by
Iorio, Alfonso
;
Edginton, Andrea N.
;
Blanchette, Victor
;
Blatny, Jan
;
Boban, Ana
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
July 2018 2(3):535-548
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7 . Academic Journal
A high-throughput sequencing test for diagnosing inherited bleeding, thrombotic, and platelet disorders
저자
by
Simeoni, Ilenia
;
Stephens, Jonathan C.
;
Hu, Fengyuan
;
Deevi, Sri V.V.
;
Megy, Karyn
, et al.
소스
In
Blood
9 June 2016 127(23):2791-2803
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7 . Academic Journal
Factor VIII brand and the incidence of factor VIII inhibitors in previously untreated UK children with severe hemophilia A, 2000-2011
저자
by
Collins, Peter W.
;
Palmer, Benedict P.
;
Chalmers, Elizabeth A.
;
Hart, Daniel P.
;
Liesner, Ri
, et al.
소스
In
Blood
27 November 2014 124(23):3389-3397
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7 . Academic Journal
The factor VIII treatment history of non‐severe hemophilia A—Response from original authors Abdi et al
저자
by
Kloosterman, Fabienne R.
;
Abdi, Amal
;
Gouw, Samantha C.
;
Hart, Daniel P.
;
Fijnvandraat, Karin
.
소스
In
Journal of Thrombosis and Haemostasis
October 2021 19(10):2642-2644
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7 . Academic Journal
Emicizumab prophylaxis in haemophilia A with inhibitors: Three years follow‐up from the UK Haemophilia Centre Doctors' Organisation (UKHCDO).
저자
by
Wall, Caroline
;
Xiang, Hua
;
Palmer, Ben
;
Chalmers, Elizabeth
;
Chowdary, Pratima
, et al.
소스
Haemophilia
. May2023, Vol. 29 Issue 3, p743-752. 10p. 1 Diagram, 3 Charts, 3 Graphs.
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7 . Academic Journal
WT1-specific T cell receptor gene therapy: Improving TCR function in transduced T cells
저자
by
Stauss, Hans J.
;
Thomas, Sharyn
;
Cesco-Gaspere, Michela
;
Hart, Daniel P.
;
Xue, Shao-An
, et al.
소스
In
Blood Cells, Molecules and Diseases
2008 40(1):113-116
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7 . Academic Journal
Considerations for shared decision management in previously untreated patients with hemophilia A or B.
저자
by
Astermark, Jan
;
Blatný, Jan
;
Königs, Christoph
;
Hermans, Cédric
;
Jiménez-Yuste, Victor
, et al.
소스
Therapeutic Advances in Hematology; Jan-Dec2023, Vol. 14, p1-21, 21p
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7 . Academic Journal
Dose-escalated donor lymphocyte infusions following reduced intensity transplantation: toxicity, chimerism, and disease responses
저자
by
Peggs, Karl S.
;
Thomson, Kirsty
;
Hart, Daniel P.
;
Geary, Johanne
;
Morris, Emma C.
, et al.
소스
In
Blood
15 February 2004 103(4):1548-1556
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7 . Academic Journal
Commentary on “Development of a novel fully functional coagulation factor VIII with reduced immunogenicity utilizing an in silico prediction and deimmunization approach” ‐ Will we ever be able to avoid inhibitor formation in hemophilia A?
저자
by
Hart, Daniel P.
.
소스
In
Journal of Thrombosis and Haemostasis
September 2021 19(9):2125-2126
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3 . Academic Journal
Rare variants in GP1BB are responsible for autosomal dominant macrothrombocytopenia
저자
by
Sivapalaratnam, Suthesh
;
Westbury, Sarah K.
;
Stephens, Jonathan C.
;
Greene, Daniel
;
Downes, Kate
, et al.
소스
In
Blood
26 January 2017 129(4):520-524
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