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1 . Academic Journal
Predictors of 6-year event-free survival in Alagille syndrome patients treated with maralixibat, an ileal bile acid transporter inhibitor.
저자
by
Sokol, Ronald J.
;
Gonzales, Emmanuel M.
;
Kamath, Binita M.
;
Baker, Alastair
;
Vig, Pamela
, et al.
소스
Hepatology (02709139); Dec2023, Vol. 78 Issue 6, p1698-1710, 13p
Web of Science
Scopus
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7 . Academic Journal
Natural history of liver disease in a large international cohort of children with Alagille syndrome: Results from the GALA study.
저자
by
Vandriel, Shannon M.
;
Li, Li‐Ting
;
She, Huiyu
;
Wang, Jian‐She
;
Gilbert, Melissa A.
, et al.
소스
Hepatology (02709139); Feb2023, Vol. 77 Issue 2, p512-529, 18p
Web of Science
Scopus
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7 .
Application of real-world evidence analytics: A 6-year event-free survival analysis in alagille syndrome of the gala clinical research database and maralixibat treated patients
저자
by
Hansen, Bettina E.
;
Vandriel, Shannon M.
;
Vig, Pamela
;
Garner, Will
;
Li, Li-Ting
, et al.
소스
Hepatology, 74(6), 1387A-1389A. Wiley
Scopus
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7 .
Relationships between changes in autotaxin, pruritus, and serum bile acids after odevixibat treatment in patients with progressive familial intrahepatic cholestasis: Data from a pooled analysis
저자
by
Gonzales, Emmanuel M.
;
Thompson, Richard J.
;
Kamath, Binita
;
Lacaille, Florence
;
Lainka, Elke
, et al.
소스
Hepatology, 74, 30A-31A. Wiley
Scopus
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7 .
HEPATIC PARAMETERS, GROWTH, AND SLEEP WITH RESPONDERS AND NONRESPONDERS TO ODEVIXIBAT TREATMENT: POOLED DATA FROM THE PEDFIC 1 AND PEDFIC 2 STUDIES IN CHILDREN WITH PROGRESSIVE FAMILIAL INTRAHEPATIC CHOLESTASIS
저자
by
McKiernan, Patrick James
;
Sturm, Ekkehard
;
Kamath, Binita
;
Horn, Patrick
;
Kjems, Lise
, et al.
소스
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7 .
THE PRESENCE OF A TRUNCATING MUTATION IN ABCB11 ABROGATES THE BENEFICIAL EFFECT OF A RESIDUAL FUNCTION MUTATION ON THE COURSE OF SEVERE BILE SALT EXPORT PUMP DEFICIENCY
저자
by
Felzen, Antonia
;
van Wessel, Daan
;
Thompson, Richard J.
;
Gonzales, Emmanuel M.
;
Jankowska, Irena
, et al.
소스
Hepatology, 72, 884A-886A. Wiley
Scopus
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7 .
NATIVE LIVER SURVIVAL IN PATIENTS WITH FIC1 DEFICIENCY: IMPACT OF GENOTYPE, SERUM BILE ACID CONCENTRATIONS AND SURGICAL BILIARY DIVERSION
저자
by
van Wessel, Daan
;
Thompson, Richard J.
;
Gonzales, Emmanuel M.
;
Jankowska, Irena
;
Shneider, Benjamin L.
, et al.
소스
Hepatology, 72, 878A-880A. Wiley
Scopus
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7 . Academic Journal
PHENOTYPIC DIVERGENCE OF JAGGED1 AND NOTCH2-ASSOCIATED ALAGILLE SYNDROME: RESULTS FROM THE INTERNATIONAL MULTICENTER GALA STUDY GROUP
저자
by
Vandriel, Shannon
;
Li, Liting
;
She, Huiyu
;
Wang, Jian-She
;
Gilbert, Melissa A.
, et al.
소스
HEPATOLOGY
; NOV 2020, 72 p882A-p884A, 3p. Supplement: 1
Scopus
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7 .
Genotype phenotype relationships in patients with relatively mild mutations in ABCB11: results from the napped consortium
저자
by
van Wesssel, Daan
;
Thompson, Richard J.
;
Gonzales, Emmanuel M.
;
Jankowska, Irena
;
Sokal, Etienne
, et al.
소스
Hepatology, Vol. November, p. abstract 69 (2019)
Open Access (OpenAIRE)
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7 .
Predictors of long-term normal histology on protocol allograft biopsies
저자
by
Rajanayagam, Jeremy K.
;
Hartleif, Steffen
;
Haller, Wolfram
;
Debray, Dominique
;
Verkade, Henkjan J.
, et al.
소스
Hepatology, 66, 926A-927A. Wiley
Scopus
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