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1 . Academic Journal
Anti-CD45 PBD-based antibody-drug conjugates are effective targeted conditioning agents for gene therapy and stem cell transplant
저자
by
Yeung, Jenny
;
Liao, Aiyin
;
Shaw, Matthew
;
Silva, Soraia
;
Vetharoy, Winston
, et al.
소스
In
Molecular Therapy
March 2024
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7 . Academic Journal
Targeting the central nervous system in lysosomal storage diseases: Strategies to deliver therapeutics across the blood-brain barrier
저자
by
Critchley, Bethan J.
;
Gaspar, H. Bobby
;
Benedetti, Sara
.
소스
In
Molecular Therapy
1 March 2023 31(3):657-675
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5 . Academic Journal
Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy
저자
by
Bradford, Kathryn L.
;
Liu, Siyu
;
Krajinovic, Maja
;
Ansari, Marc
;
Garabedian, Elizabeth
, et al.
소스
In
Biology of Blood and Marrow Transplantation
October 2020 26(10):1819-1827
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7 . Academic Journal
Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency
저자
by
Kohn, Donald B.
;
Hershfield, Michael S.
;
Puck, Jennifer M.
;
Aiuti, Alessandro
;
Blincoe, Annaliesse
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
March 2019 143(3):852-863
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7 . Academic Journal
Mutations in linker for activation of T cells (LAT) lead to a novel form of severe combined immunodeficiency
저자
by
Bacchelli, Chiara
;
Moretti, Federico A.
;
Carmo, Marlene
;
Adams, Stuart
;
Stanescu, Horia C.
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
February 2017 139(2):634-642
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7 . Academic Journal
Hematopoietic stem cell transplantation outcomes for 11 patients with dedicator of cytokinesis 8 deficiency
저자
by
Al-Herz, Waleed
;
Chu, Julia I.
;
van der Spek, Jet
;
Raghupathy, Raj
;
Massaad, Michel J.
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
September 2016 138(3):852-859
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7 . Academic Journal
Treating Immunodeficiency through HSC Gene Therapy
저자
by
Booth, Claire
;
Gaspar, H. Bobby
;
Thrasher, Adrian J.
.
소스
In
Trends in Molecular Medicine
April 2016 22(4):317-327
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5 . Academic Journal
Multicenter experience in hematopoietic stem cell transplantation for serious complications of common variable immunodeficiency
저자
by
Wehr, Claudia
;
Gennery, Andrew R.
;
Lindemans, Caroline
;
Schulz, Ansgar
;
Hoenig, Manfred
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
April 2015 135(4):988-997
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7 . Academic Journal
How I treat severe combined immunodeficiency
저자
by
Gaspar, H. Bobby
;
Qasim, Waseem
;
Davies, E. Graham
;
Rao, Kanchan
;
Amrolia, Persis J.
, et al.
소스
In
Blood
28 November 2013 122(23):3749-3758
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7 . Academic Journal
Outcome of hematopoietic stem cell transplantation for adenosine deaminase–deficient severe combined immunodeficiency
저자
by
Hassan, Amel
;
Booth, Claire
;
Brightwell, Alex
;
Allwood, Zoe
;
Veys, Paul
, et al.
소스
In
Blood
25 October 2012 120(17):3615-3624
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