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1 . Academic Journal
Deciphering conundrums of adeno-associated virus liver-directed gene therapy: focus on hemophilia
저자
by
Pierce, Glenn F.
;
Fong, Sylvia
;
Long, Brian R.
;
Kaczmarek, Radoslaw
.
소스
In
Journal of Thrombosis and Haemostasis
May 2024 22(5):1263-1289
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6 . Academic Journal
Adeno-associated viruses for gene therapy – clinical implications and liver-related complications, a guide for hepatologists
저자
by
Mücke, Marcus Maximilian
;
Fong, Sylvia
;
Foster, Graham R.
;
Lillicrap, David
;
Miesbach, Wolfgang
, et al.
소스
In
Journal of Hepatology
February 2024 80(2):352-361
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7 . Academic Journal
Vector integration and fate in the hemophilia dog liver multiple years after AAV-FVIII gene transfer
저자
by
Batty, Paul
;
Fong, Sylvia
;
Franco, Matteo
;
Sihn, Choong-Ryoul
;
Swystun, Laura L.
, et al.
소스
In
Blood
February 2024
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7 . Academic Journal
Young mice administered adult doses of AAV5-hFVIII-SQ achieve therapeutic factor VIII expression into adulthood
저자
by
Zhang, Lening
;
Yates, Bridget
;
Murphy, Ryan
;
Liu, Su
;
Xie, Lin
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
8 September 2022 26:519-531
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7 . Academic Journal
Application of in-vitro-cultured primary hepatocytes to evaluate species translatability and AAV transduction mechanisms of action
저자
by
Liu, Su
;
Razon, Lisa
;
Ritchie, Olivia
;
Sihn, Choong-Ryoul
;
Handyside, Britta
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
8 September 2022 26:61-71
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7 . Academic Journal
Vector genome loss and epigenetic modifications mediate decline in transgene expression of AAV5 vectors produced in mammalian and insect cells
저자
by
Handyside, Britta
;
Ismail, Ashrafali Mohamed
;
Zhang, Lening
;
Yates, Bridget
;
Xie, Lin
, et al.
소스
In
Molecular Therapy
November 2022
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7 . Academic Journal
Adenovirus‐associated antibodies in UK cohort of hemophilia patients: A seroprevalence study of the presence of adenovirus‐associated virus vector–serotypes AAV5 and AAV8 neutralizing activity and antibodies in patients with hemophilia A
저자
by
Stanford, Sophia
;
Pink, Ruth
;
Creagh, Desmond
;
Clark, Amanda
;
Lowe, Gillian
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
April 2019 3(2):261-267
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7 . Academic Journal
Valoctocogene roxaparvovec gene transfer in participants with HIV
저자
by
Ragni, Margaret V.
;
Majerus, Elaine
;
Fong, Sylvia
;
Yates, Bridget
;
Scheeler, Stephen
, et al.
소스
In
Blood Advances
25 April 2023 7(8):1525-1530
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7 . Academic Journal
Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression.
저자
by
Handyside, Britta
;
Zhang, Lening
;
Yates, Bridget
;
Xie, Lin
;
Ismail, Ashrafali Mohamed
, et al.
소스
Human Gene Therapy
. Jan2024, Vol. 35 Issue 1/2, p36-47. 12p.
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7 . Academic Journal
Id genes and proteins as promising targets in cancer therapy
저자
by
Fong, Sylvia
;
Debs, Robert J.
;
Desprez, Pierre-Yves
.
소스
In
Trends in Molecular Medicine
2004 10(8):387-392
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