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1 . Academic Journal
Convergence of patient- and physician-reported outcomes in the French National Registry of Facioscapulohumeral Dystrophy
저자
by
Benoît Sanson
;
Caroline Stalens
;
Céline Guien
;
Luisa Villa
;
Catherine Eng
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-12 (2022)
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7 . Academic Journal
Identification of wheelchair seating criteria in adults with neuromuscular diseases: A Delphi study.
저자
by
Elise Dupitier
;
Manon Voisin
;
Caroline Stalens
;
Pascal Laforêt
;
Samuel Pouplin
.
소스
PLoS ONE, Vol 18, Iss 9, p e0290627 (2023)
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7 . Academic Journal
Parents' dilemma: A therapeutic decision for children with spinal muscular atrophy (SMA) type 1
저자
by
Sophie Boursange
;
Marco Araneda
;
Caroline Stalens
;
Isabelle Desguerre
;
Christine Barnerias
, et al.
소스
Frontiers in Pediatrics, Vol 10 (2022)
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7 .
Improved Cardiac Outcomes by Early Treatment with Angiotensin-Converting Enzyme Inhibitors in Becker Muscular Dystrophy
저자
by
Nawal Berber
;
Pascal Laforêt
;
Bertrand Fontaine
;
Marion Masingue
;
Leslie Motté
, et al.
소스
Journal of Neuromuscular Diseases
Journal of Neuromuscular Diseases, 2021, 8 (4), pp.495-502. ⟨10.3233/jnd-200620⟩
Journal of Neuromuscular Diseases, IOS Press, 2021, 8 (4), pp.495-502. ⟨10.3233/jnd-200620⟩
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7 .
Cardiac Outcomes in Adults With Mitochondrial Diseases
저자
by
Konstantinos Savvatis
;
Christoffer Rasmus Vissing
;
Lori Klouvi
;
Anca Florian
;
Mehjabin Rahman
, et al.
소스
Journal of the American College of Cardiology
Journal of the American College of Cardiology, 2022, 80 (15), pp.1421-1430. ⟨10.1016/j.jacc.2022.08.716⟩
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7 .
Impact of Mechanical Ventilation Methods on the Life Perception of Subjects With Duchenne Muscular Dystrophy: French Cross-Sectional Survey
저자
by
Caroline Stalens
;
Christian Devaux
;
Frédéric Lofaso
;
Sandrine Segovia-Kueny
;
Christian Réveillère
, et al.
소스
Respiratory Care
Respiratory Care, Daedalus Enterprises Inc, 2020, 65 (11), pp.1712-1720. ⟨10.4187/respcare.07131⟩
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7 .
Development and Validation of a New Risk Prediction Score for Life-Threatening Ventricular Tachyarrhythmias in Laminopathies
저자
by
Mélanie Fradin
;
Nicolas Sadoul
;
Xavier Waintraub
;
Didier Klug
;
Albert Hagège
, et al.
소스
Circulation
Circulation, 2019, 140 (4), pp.293-302. ⟨10.1161/CIRCULATIONAHA.118.039410⟩
Circulation, American Heart Association, 2019, 140 (4), pp.293-302. ⟨10.1161/CIRCULATIONAHA.118.039410⟩
Circulation, 140(4), 293-302. LIPPINCOTT WILLIAMS & WILKINS
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7 .
Bientôt une étude pilote pour le premier dépistage génétique à la naissance en France !
저자
by
Caroline Stalens
;
Vincent Laugel
;
Caroline Espil-Taris
;
Christian Cottet
.
소스
Les Cahiers de Myologie
. :3-4
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6 .
Participation de l’AFM-Téléthon (2012-2016) au Réseau Européen Help Lines d’Eurordis
저자
by
Caroline Stalens
;
Tuy Nga Brignol
;
François Houÿez
.
소스
Les Cahiers de Myologie
. :39-42
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5 .
Understanding European patient expectations towards current therapeutic development in spinal muscular atrophy
저자
by
Nicole Gusset
;
Caroline Stalens
;
Mencia de Lemus
;
Marie-Christine Ouillade
;
Eva Stumpe
, et al.
소스
Neuromuscular disorders : NMD
. 31(5)
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