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1 . Academic Journal
Hepatic Glycogen Storage Diseases Toward One Global Collaborative Network
저자
by
Derks, Terry G. J.
;
Nemeth, Antal
;
Adrian, Katrin
;
Arnell, Henrik
;
Roskjær, Ann Bech
, et al.
소스
Journal of Inborn Errors of Metabolism and Screening
. January 2017 5
Open Access (SciELO)
Scopus
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7 . Academic Journal
Genotype-phenotype relationships of truncating mutations, p.E297G and p.D482G in bile salt export pump deficiency
저자
by
Felzen, Antonia
;
van Wessel, Daan B.E.
;
Gonzales, Emmanuel
;
Thompson, Richard J.
;
Jankowska, Irena
, et al.
소스
In
JHEP Reports
February 2023 5(2)
Full Text (Clinical Key)
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7 . Academic Journal
Odevixibat treatment in progressive familial intrahepatic cholestasis: a randomised, placebo-controlled, phase 3 trial
저자
by
Thompson, Richard J
;
Arnell, Henrik
;
Artan, Reha
;
Baumann, Ulrich
;
Calvo, Pier Luigi
, et al.
소스
In
The Lancet Gastroenterology & Hepatology
September 2022 7(9):830-842
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7 . Academic Journal
THU-291 - Serum bile acids are associated with native liver survival in patients with Alagille syndrome: results from the GALA study group
저자
by
Murillo Perez, Carla Fiorella
;
Vandriel, Shannon M.
;
Wang, Jian-She
;
Liting, Li
;
She, Huiyu
, et al.
소스
In
Journal of Hepatology
June 2023 78 Supplement 1:S971-S973
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7 . Academic Journal
Internet-delivered cognitive behavior therapy for adolescents with functional gastrointestinal disorders — An open trial
저자
by
Bonnert, Marianne
;
Ljótsson, Brjánn
;
Hedman, Erik
;
Andersson, Johanna
;
Arnell, Henrik
, et al.
소스
In
Internet Interventions - The application of information technology in mental and behavioural
July 2014 1(3):141-148
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7 . Academic Journal
THU-289 - Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database
저자
by
Hansen, Bettina
;
Valcheva, Velichka
;
Yu, Qifeng
;
van Wessel, Daan
;
Thompson, Richard
, et al.
소스
In
Journal of Hepatology
June 2023 78 Supplement 1:S969-S970
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7 . Academic Journal
Development of a core outcome set for pediatric chronic intestinal failure.
저자
by
Demirok, Aysenur
;
Nagelkerke, Sjoerd C. J.
;
Benninga, Marc A.
;
Köglmeier, Jutta
;
Mutanen, Annika
, et al.
소스
JPEN Journal of Parenteral & Enteral Nutrition; Mar2023, Vol. 47 Issue 3, p364-371, 8p
Web of Science
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7 . Academic Journal
PS-194-Effects of the ileal bile acid transport inhibitor A4250 on serum bile acids, pruritus and sleep in patients with Alagille syndrome: Phase 2 study results
저자
by
Baumann, Ulrich
;
Sturm, Ekkehard
;
Lacaille, Florence
;
Gonzales, Emmanuel
;
Arnell, Henrik
, et al.
소스
In
Journal of Hepatology
April 2019 70(1) Supplement:e120-e120
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7 . Academic Journal
PS-195-Predicting long-term outcome after surgical biliary diversion in Bsep-deficiency patients: Results from the NAPPED consortium
저자
by
Wessel, Daan van
;
Thompson, Richard
;
Grammatikopoulos, Tassos
;
Kadaristiana, Agustina
;
Jankowska, Irena
, et al.
소스
In
Journal of Hepatology
April 2019 70(1) Supplement:e121-e121
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7 . Academic Journal
Non-alcoholic fatty liver disease in children and young adults is associated with increased long-term mortality.
저자
by
Simon, Tracey G.
;
Roelstraete, Bjorn
;
Hartjes, Kayla
;
Shah, Uzma
;
Khalili, Hamed
, et al.
소스
Journal of Hepatology
. Nov2021, Vol. 75 Issue 5, p1034-1041. 8p.
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