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21 . Academic Journal
Induction of T-Cell Infiltration and Programmed Death Ligand 2 Expression by Adeno-Associated Virus in Rhesus Macaque Skeletal Muscle and Modulation by Prednisone.
저자
by
Cramer, Megan L.
;
Shao, Guohong
;
Rodino-Klapac, Louise R.
;
Chicoine, Louis G.
;
Martin, Paul T.
.
소스
Human Gene Therapy
. Jun2017, Vol. 28 Issue 6, p493-509. 17p.
Scopus
Web of Science
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27 . Academic Journal
Defective membrane fusion and repair in Anoctamin5-deficient muscular dystrophy.
저자
by
Griffin, Danielle A.
;
Johnson, Ryan W.
;
Whitlock, Jarred M.
;
Pozsgai, Eric R.
;
Heller, Kristin N.
, et al.
소스
Human Molecular Genetics; 5/15/2016, Vol. 25 Issue 10, p1900-1911, 12p
Full Text (OUP)
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27 . Academic Journal
Human α7 Integrin Gene ( ITGA7) Delivered by Adeno-Associated Virus Extends Survival of Severely Affected Dystrophin/Utrophin-Deficient Mice.
저자
by
Heller, Kristin N.
;
Montgomery, Chrystal L.
;
Shontz, Kimberly M.
;
Clark, K. Reed
;
Mendell, Jerry R.
, et al.
소스
Human Gene Therapy
. Oct2015, Vol. 26 Issue 10, p647-656. 10p.
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27 . Book
Dystrophinopathies.
저자
by
Sahenk, Zarife
;
Rodino-Klapac, Louise R.
.
소스
Neuromuscular Disorders in Clinical Practice; 2014, p1207-1229, 23p
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24 . Academic Journal
AAV.Dysferlin Overlap Vectors Restore Function in Dysferlinopathy Animal Models.
저자
by
Sondergaard, Patricia C.
;
Griffin, Danielle A.
;
Pozsgai, Eric R.
;
Johnson, Ryan W.
;
Grose, William E.
, et al.
소스
Annals of Clinical & Translational Neurology
. Mar2015, Vol. 2 Issue 3, p256-270. 15p.
Open Access (Wiley)
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27 . Book
AAV-Mediated Gene Therapy to the Isolated Limb in Rhesus Macaques.
저자
by
Rodino-Klapac, Louise R.
;
Montgomery, Chrystal L.
;
Mendell, Jerry R.
;
Chicoine, Louis G.
.
소스
Muscle Gene Therapy; 2011, p287-298, 12p
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26 . Academic Journal
Micro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model
저자
by
Rodino-Klapac, Louise R.
;
Janssen, Paul M. L.
;
Shontz, Kimberly M.
;
Canan, Benjamin
;
Montgomery, Chrystal L.
, et al.
소스
Human Molecular Genetics
. Dec 15, 2013 22(24):4929-4937
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27 . Academic Journal
Eteplirsen for the treatment of Duchenne muscular dystrophy
저자
by
Mendell, Jerry R.
;
Rodino-Klapac, Louise R.
;
Sahenk, Zarife
;
Roush, Kandice
;
Bird, Loren
, et al.
소스
Annals of Neurology
. Nov 01, 2013 74(5):637-647
Full Text (Wiley)
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27 . Periodical
Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy
저자
by
Al-Zaidy, Samiah A.
;
Sahenk, Zarife
;
Rodino-Klapac, Louise R.
;
Kaspar, Brian
;
Mendell, Jerry R.
.
소스
Journal of Neuromuscular Diseases; September 2015, Vol. 2 Issue: 3 p185-192, 8p
Scopus
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27 . Academic Journal
Vascular Delivery of rAAVrh74.MCK.GALGT2 to the Gastrocnemius Muscle of the Rhesus Macaque Stimulates the Expression of Dystrophin and Laminin α2 Surrogates.
저자
by
Chicoine, Louis G.
;
Rodino-Klapac, Louise R.
;
Shao, Guohong
;
Xu, Rui
;
Bremer, William G.
, et al.
소스
Molecular Therapy
. Apr2014, Vol. 22 Issue 4, p713-724. 12p.
Full Text (ScienceDirect)
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