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21 .
Vascular Smooth Muscle Cells From Hypertensive Patient-Derived Induced Pluripotent Stem Cells to Advance Hypertension Pharmacogenomics
저자
by
Santiago D. Carrasquilla
;
Nihal El Rouby
;
Julie A. Johnson
;
Rhonda M. Cooper-DeHoff
;
Naohiro Terada
, et al.
소스
Stem cells translational medicine
. 4(12)
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27 .
Efficient Gene Editing in Pluripotent Stem Cells by Bacterial Injection of Transcription Activator-Like Effector Nuclease Proteins
저자
by
Jingyue Jia
;
Yongxin Jin
;
Shouguang Jin
;
Naohiro Terada
;
Fang Bai
, et al.
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27 .
182. Characterization and AAV-Mediated Correction of Xeroderma Pigmentosum-Cockayne Syndrome (XP/CS)
저자
by
Skylar A. Rizzo
;
Naohiro Terada
;
Christina A. Pacak
;
Fowzan S. Alkuraya
;
Amy Donate
, et al.
소스
Molecular Therapy
. 23
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27 .
A practical guide to induced pluripotent stem cell research using patient samples
저자
by
Naohiro Terada
;
Nikolett M. Biel
;
Akihiro Umezawa
;
Shouguang Jin
;
Takashi Hamazaki
, et al.
소스
Laboratory investigation; a journal of technical methods and pathology
. 95(1)
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27 .
E2f6-mediated repression of the meiotic Stag3 and Smc1β genes during early embryonic development requires Ezh2 and not the de novo methyltransferase Dnmt3b
저자
by
Naohiro Terada
;
Takashi Hamazaki
;
Milena Leseva
;
Amy L Rosenbluth
;
Katherine E. Santostefano
.
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27 .
Generation of human induced pluripotent stem cells to model spinocerebellar ataxia type 2 in vitro
저자
by
Jilin Liu
;
Takashi Hamazaki
;
Guangbin Xia
;
S. H. Subramony
;
Tetsuo Ashizawa
, et al.
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27 .
360. Genotype/Phenotype Correlation of Cellular Function and AAV-Mediated Gene Delivery to Treat Xeroderma Pigmentosum - Cockayne Syndrome (XP - CS)
저자
by
Amy Donate
;
Peter B. Kang
;
Skylar A. Rizzo
;
Fowzan S. Alkuraya
;
Christina A. Pacak
, et al.
소스
Molecular Therapy
. 24:S144
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27 .
191. Frataxin: A Putative Biomarker for Minimal Effective Dosage of AAV Gene Therapy
저자
by
Nathalie Clemente
;
Barry J. Byrne
;
Amy Donate
;
Christina A. Pacak
;
Denise A. Cloutier
, et al.
소스
Molecular Therapy
. 23:S76
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27 .
187. AAV Delivery of Tafazzin for the Correction of Mitochondrial Dysfunction in Barth Syndrome Using IPS Differentiated Cardiomyocytes
저자
by
Todd Cade
;
Skylar A. Rizzo
;
Bennett J. Gosiker
;
Alfred S. Lewin
;
Amy Donate
, et al.
소스
Molecular Therapy
. 23:S75
Open Access (OpenAIRE)
Full Text (ScienceDirect O/A)
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