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11 . Academic Journal
Treatment of skeletal and non-skeletal alterations of Mucopolysaccharidosis type IVA by AAV-mediated gene therapy
저자
by
Joan Bertolin
;
Víctor Sánchez
;
Albert Ribera
;
Maria Luisa Jaén
;
Miquel Garcia
, et al.
소스
Nature Communications, Vol 12, Iss 1, Pp 1-14 (2021)
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17 . Academic Journal
CDK4 is an essential insulin effector in adipocytes
저자
by
Sylviane Lagarrigue
;
Isabel C. Lopez-Mejia
;
Pierre-Damien Denechaud
;
Xavier Escoté
;
Judit Castillo-Armengol
, et al.
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The Journal of Clinical Investigation, Vol 132, Iss 13 (2022)
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17 . Academic Journal
The Deep Genome Project
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by
K. C. Kent Lloyd
;
David J. Adams
;
Gareth Baynam
;
Arthur L. Beaudet
;
Fatima Bosch
, et al.
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Genome Biology, Vol 21, Iss 1, Pp 1-6 (2020)
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17 . Academic Journal
BMP4 gene therapy enhances insulin sensitivity but not adipose tissue browning in obese mice
저자
by
Jenny M. Hoffmann
;
John R. Grünberg
;
Ann Hammarstedt
;
Tobias Kroon
;
Thomas U. Greiner
, et al.
소스
Molecular Metabolism, Vol 32, Iss , Pp 15-26 (2020)
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17 . Academic Journal
Cannabinoid type-1 receptor blockade restores neurological phenotypes in two models for Down syndrome
저자
by
Alba Navarro-Romero
;
Anna Vázquez-Oliver
;
Maria Gomis-González
;
Carlos Garzón-Montesinos
;
Rafael Falcón-Moya
, et al.
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Neurobiology of Disease, Vol 125, Iss , Pp 92-106 (2019)
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17 . Academic Journal
Adult mice are unresponsive to AAV8-Gremlin1 gene therapy targeting the liver.
저자
by
Roxana Khatib Shahidi
;
Jenny M Hoffmann
;
Shahram Hedjazifar
;
Laurianne Bonnet
;
Ritesh K Baboota
, et al.
소스
PLoS ONE, Vol 16, Iss 2, p e0247300 (2021)
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17 . Academic Journal
Bone Morphogenetic Protein 4 Gene Therapy in Mice Inhibits Myeloma Tumor Growth, But Has a Negative Impact on Bone
저자
by
Marita Westhrin
;
Toril Holien
;
Muhammad Zahoor
;
Siv Helen Moen
;
Glenn Buene
, et al.
소스
JBMR Plus, Vol 4, Iss 1, Pp n/a-n/a (2020)
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17 . Academic Journal
Identification of genetic elements in metabolism by high-throughput mouse phenotyping
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by
Jan Rozman
;
Birgit Rathkolb
;
Manuela A. Oestereicher
;
Christine Schütt
;
Aakash Chavan Ravindranath
, et al.
소스
Nature Communications, Vol 9, Iss 1, Pp 1-16 (2018)
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17 . Academic Journal
Long-Term Efficacy and Safety of Insulin and Glucokinase Gene Therapy for Diabetes: 8-Year Follow-Up in Dogs
저자
by
Maria Luisa Jaén
;
Laia Vilà
;
Ivet Elias
;
Veronica Jimenez
;
Jordi Rodó
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 1-7 (2017)
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17 . Academic Journal
BMP4 Gene Therapy in Mature Mice Reduces BAT Activation but Protects from Obesity by Browning Subcutaneous Adipose Tissue
저자
by
Jenny M. Hoffmann
;
John R. Grünberg
;
Christopher Church
;
Ivet Elias
;
Vilborg Palsdottir
, et al.
소스
Cell Reports, Vol 20, Iss 5, Pp 1038-1049 (2017)
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