AAV8 gene therapy reverses cardiac pathology and prevents early mortality in a mouse model of Friedreich’s ataxia
- Resource Type
- Article
- Authors
- Chang, Joshua C.; Ryan, Molly R.; Stark, Marie C.; Liu, Su; Purushothaman, Pravinkumar; Bolan, Fria; Johnson, Caitlin A.; Champe, Mark; Meng, Hui; Lawlor, Michael W.; Halawani, Sarah; Ngaba, Lucie V.; Lynch, David R.; Davis, Crystal; Gonzalo-Gil, Elena; Lutz, Cathleen; Urbinati, Fabrizia; Medicherla, Bala; Fonck, Carlos
- Source
- In Molecular Therapy - Methods & Clinical Development 14 March 2024 32(1)
- Subject
- Language
- ISSN
- 2329-0501