Intrathymic AAV delivery results in therapeutic site-specific integration at TCR loci in mice
- Resource Type
- Article
- Authors
- Calabria, Andrea; Cipriani, Carlo; Spinozzi, Giulio; Rudilosso, Laura; Esposito, Simona; Benedicenti, Fabrizio; Albertini, Alessandra; Pouzolles, Marie; Luoni, Mirko; Giannelli, Serena; Broccoli, Vania; Guilbaud, Mickael; Adjali, Oumeya; Taylor, Naomi; Zimmermann, Valérie S.; Montini, Eugenio; Cesana, Daniela
- Source
- In Blood January 2023
- Subject
- Gene Therapy
- Language
- ISSN
- 0006-4971