Brain delivery and efficacy of an intravenously-administered lysosomal enzyme using a blood-brain barrier transport vehicle.
- Resource Type
- Article
- Authors
- Henry, Anastasia G.; Ullman, Julie; Arguello, Annie; Getz, Jennifer; Bhalla, Akhil; Mahon, Cathal; Wang, Junhua; Giese, Tina; Bedard, Catherine; Blumenfeld, Jessica; Ravi, Ritesh; Nugent, Alicia; Lianoglou, Steve; Dennis, Mark; Gunasekaran, Kannan; Srivastava, Ankita; Henne, Kirk; Thorne, Robert; Di Paolo, Gilbert; Astarita, Giuseppe
- Source
- Molecular Genetics & Metabolism. Feb2020, Vol. 129 Issue 2, pS72-S72. 1p.
- Subject
- *BLOOD-brain barrier
*TRANSPORT vehicles
*ENZYMES
*GENE expression profiling
- Language
- ISSN
- 1096-7192