Unexpected Mutations by CRISPR-Cas9 CTG Repeat Excision in Myotonic Dystrophy and Use of CRISPR Interference as an Alternative Approach
- Resource Type
- Journal
- Authors
- Ikeda, Miki; Taniguchi-Ikeda, Mariko; Kato, Takema; Shinkai, Yasuko; Tanaka, Sonoko; Hagiwara, Hiroki; Sasaki, Naomichi; Masaki, Toshihiro; Matsumura, Kiichiro; Sonoo, Masahiro; Kurahashi, Hiroki; Saito, Fumiaki
- Source
- MOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT; SEP 11 2020, 18 p131-p144, 14p.
- Subject
- Language
- English
- ISSN
- 23290501