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1 . Academic Journal
Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiency
저자
by
Migliavacca, Maddalena
;
Barzaghi, Federica
;
Fossati, Claudia
;
Rancoita, Paola M. V.
;
Gabaldo, Michela
, et al.
소스
Nature Medicine
. 30(2):488-497
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7 . Academic Journal
A case of T-cell acute lymphoblastic leukemia in retroviral gene therapy for ADA-SCID
저자
by
Daniela Cesana
;
Maria Pia Cicalese
;
Andrea Calabria
;
Pietro Merli
;
Roberta Caruso
, et al.
소스
Nature Communications, Vol 15, Iss 1, Pp 1-18 (2024)
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7 . Academic Journal
Lack of association between classical HLA genes and asymptomatic SARS-CoV-2 infection
저자
by
Astrid Marchal
;
Elizabeth T. Cirulli
;
Iva Neveux
;
Evangelos Bellos
;
Ryan S. Thwaites
, et al.
소스
HGG Advances, Vol 5, Iss 3, Pp 100300- (2024)
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7 . Academic Journal
Gene therapy for rare haematological and neurometabolic paediatric diseases
저자
by
Vera Gallo
;
Alessandro Aiuti
.
소스
Global Pediatrics, Vol 9, Iss , Pp 100196- (2024)
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4 . Academic Journal
Hematopoietic reconstitution dynamics of mobilized- and bone marrow-derived human hematopoietic stem cells after gene therapy
저자
by
Scala, Serena
;
Ferrua, Francesca
;
Basso-Ricci, Luca
;
Dionisio, Francesca
;
Omrani, Maryam
, et al.
소스
Nature Communications
. 14(1)
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7 . Academic Journal
Rare predicted loss-of-function variants of type I IFN immunity genes are associated with life-threatening COVID-19
저자
by
Matuozzo, Daniela
;
Talouarn, Estelle
;
Marchal, Astrid
;
Zhang, Peng
;
Manry, Jeremy
, et al.
소스
Genome Medicine
. 15(1)
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7 . Academic Journal
Correction: Rare predicted loss-of-function variants of type I IFN immunity genes are associated with life-threatening COVID-19
저자
by
Daniela Matuozzo
;
Estelle Talouarn
;
Astrid Marchal
;
Peng Zhang
;
Jeremy Manry
, et al.
소스
Genome Medicine, Vol 16, Iss 1, Pp 1-3 (2024)
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7 . Academic Journal
Lack of association between classical HLA genes and asymptomatic SARS-CoV-2 infection
저자
by
Abel, Laurent
;
Aiuti, Alessandro
;
Al-Muhsen, Saleh
;
Al-Mulla, Fahd
;
Amara, Ali
, et al.
소스
In
Human Genetics and Genomics Advances
18 July 2024 5(3)
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7 . Academic Journal
Wiskott-Aldrich syndrome: a study of 577 patients defines the genotype as a biomarker for disease severity and survival
저자
by
Vallée, Tanja C.
;
Glasmacher, Jannik S.
;
Buchner, Hannes
;
Arkwright, Peter D.
;
Behrends, Uta
, et al.
소스
In
Blood
13 June 2024 143(24):2504-2516
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7 . Academic Journal
Circulating hematopoietic stem/progenitor cell subsets contribute to human hematopoietic homeostasis
저자
by
Quaranta, Pamela
;
Basso-Ricci, Luca
;
Jofra Hernandez, Raisa
;
Pacini, Guido
;
Naldini, Matteo Maria
, et al.
소스
In
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9 May 2024 143(19):1937-1952
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