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1 . Academic Journal
Glycosylation of recombinant adeno-associated virus serotype 6
저자
by
Yuki Yamaguchi
;
Kentaro Ishii
;
Sachiko Koizumi
;
Hiroaki Sakaue
;
Takahiro Maruno
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 2, Pp 101256- (2024)
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7 . Academic Journal
Efficient gene transduction in pigs and macaques with the engineered AAV vector AAV.GT5 for hemophilia B gene therapy
저자
by
Yuji Kashiwakura
;
Kazuhiro Endo
;
Atsushi Ugajin
;
Tomohiro Kikuchi
;
Shuji Hishikawa
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 30, Iss , Pp 502-514 (2023)
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7 . Academic Journal
PAM-flexible Cas9-mediated base editing of a hemophilia B mutation in induced pluripotent stem cells
저자
by
Takafumi Hiramoto
;
Yuji Kashiwakura
;
Morisada Hayakawa
;
Nemekhbayar Baatartsogt
;
Nobuhiko Kamoshita
, et al.
소스
Communications Medicine, Vol 3, Iss 1, Pp 1-12 (2023)
Open Access (DOAJ)
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7 . Academic Journal
Current status and future perspective of treatment for hemophilia / 血友病診療の現状とこれから
저자
by
Tsukasa OHMORI
;
Yuji KASHIWAKURA
;
大森 司
;
柏倉 裕志
.
소스
臨床血液 / Rinsho Ketsueki. 2023, 64(5):377
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6 . Academic Journal
The seroprevalence of neutralizing antibodies against the adeno-associated virus capsids in Japanese hemophiliacs
저자
by
Yuji Kashiwakura
;
Nemekhbayar Baatartsogt
;
Shoji Yamazaki
;
Azusa Nagao
;
Kagehiro Amano
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 27, Iss , Pp 404-414 (2022)
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7 . Academic Journal
A sensitive and reproducible cell-based assay via secNanoLuc to detect neutralizing antibody against adeno-associated virus vector capsid
저자
by
Nemekhbayar Baatartsogt
;
Yuji Kashiwakura
;
Morisada Hayakawa
;
Nobuhiko Kamoshita
;
Takafumi Hiramoto
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 22, Iss , Pp 162-171 (2021)
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7 . Academic Journal
Characterization and visualization of murine coagulation factor VIII-producing cells in vivo
저자
by
Morisada Hayakawa
;
Asuka Sakata
;
Hiroko Hayakawa
;
Hikari Matsumoto
;
Takafumi Hiramoto
, et al.
소스
Scientific Reports, Vol 11, Iss 1, Pp 1-11 (2021)
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7 . Academic Journal
Advances in gene therapy for hemophilia / 血友病に対する遺伝子治療の進歩
저자
by
Tsukasa OHMORI
;
Yuji KASHIWAKURA
;
大森 司
;
柏倉 裕志
.
소스
日本血栓止血学会誌 / Japanese Journal of Thrombosis and Hemostasis. 2021, 32(1):17
Open Access (JSTAGE)
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6 . Academic Journal
Advances in gene therapy and genome editing therapy for hemophilia / 血友病に対する遺伝子治療・ゲノム編集治療の進歩
저자
by
Tsukasa Ohmori
;
Yuji Kashiwakura
;
大森 司
;
柏倉 裕志
.
소스
日本小児血液・がん学会雑誌 / The Japanese Journal of Pediatric Hematology / Oncology. 2020, 57(3):220
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6 . Academic Journal
Development of cell-based therapy for hemophilic arthropathy / 血友病性関節症に対する遺伝子細胞治療の基礎的検討
저자
by
Yuji KASHIWAKURA
;
柏倉 裕志
.
소스
日本血栓止血学会誌 / Japanese Journal of Thrombosis and Hemostasis. 2014, 25(4):516
Open Access (JSTAGE)
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