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1 . Academic Journal
Systemic delivery of an AAV9 exon-skipping vector significantly improves or prevents features of Duchenne muscular dystrophy in the Dup2 mouse
저자
by
Wein, Nicolas
;
Vetter, Tatyana A.
;
Vulin, Adeline
;
Simmons, Tabatha R.
;
Frair, Emma C.
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
8 September 2022 26:279-293
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7 . Academic Journal
Severe PATCHED1 Deficiency in Cancer-Prone Gorlin Patient Cells Results in Intrinsic Radiosensitivity
저자
by
Vulin, Adeline
;
Sedkaoui, Melissa
;
Moratille, Sandra
;
Sevenet, Nicolas
;
Soularue, Pascal
, et al.
소스
In
International Journal of Radiation Oncology, Biology, Physics
1 October 2018 102(2):417-425
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7 . Academic Journal
The first exon duplication mouse model of Duchenne muscular dystrophy: A tool for therapeutic development
저자
by
Vulin, Adeline
;
Wein, Nicolas
;
Simmons, Tabatha R.
;
Rutherford, Andrea M.
;
Findlay, Andrew R.
, et al.
소스
In
Neuromuscular Disorders
November 2015 25(11):827-834
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7 . Academic Journal
Current Status of Antisense Oligonucleotide-Based Therapy in Neuromuscular Disorders.
저자
by
Bizot, Flavien
;
Vulin, Adeline
;
Goyenvalle, Aurélie
.
소스
Drugs
. Sep2020, Vol. 80 Issue 14, p1397-1415. 19p.
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5 . Academic Journal
X-linked muscular dystrophy in a Labrador Retriever strain: phenotypic and molecular characterisation.
저자
by
Barthélémy, Inès
;
Calmels, Nadège
;
Weiss, Robert B.
;
Tiret, Laurent
;
Vulin, Adeline
, et al.
소스
Skeletal Muscle
. 8/7/2020, Vol. 10 Issue 1, p1-22. 22p.
Open Access (BioMed Central)
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7 . Academic Journal
Déficience en PATCHED1 : une signature de radiosensibilité chez les patients atteints du syndrome de Gorlin ?
저자
by
Vulin, Adeline
;
Moratille, Sandra
;
Lamartine, Jérôme
;
Martin, Michèle
.
소스
In
Annales de dermatologie et de venereologie
December 2016 143(12) Supplement:S434-S434
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6 . Academic Journal
Human epidermal stem cells: Role in adverse skin reactions and carcinogenesis from radiation.
저자
by
Martin, Michèle T.
;
Vulin, Adeline
;
Hendry, Jolyon H.
.
소스
Mutation Research/Reviews in Mutation Research
. Oct2016 Part B, Vol. 770, p349-368. 20p.
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5 . Periodical
Efficient Skipping of Single Exon Duplications in DMDPatient-Derived Cell Lines Using an Antisense Oligonucleotide Approach
저자
by
Wein, Nicolas
;
Vulin, Adeline
;
Findlay, Andrew R.
;
Gumienny, Felecia
;
Huang, Nianyuan
, et al.
소스
Journal of Neuromuscular Diseases; August 2017, Vol. 4 Issue: 3 p199-207, 9p
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7 . Academic Journal
Dystrophin quantification: Biological and translational research implications.
저자
by
Anthony, Karen
;
Arechavala-Gomeza, Virginia
;
Taylor, Laura E
;
Vulin, Adeline
;
Kaminoh, Yuuki
, et al.
소스
Neurology; 11/25/2014, Vol. 83 Issue 22, p2062-2069, 8p
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7 . Academic Journal
Dystrophin quantification.
저자
by
Anthony, Karen
;
Arechavala-Gomeza, Virginia
;
Taylor, Laura E.
;
Vulin, Adeline
;
Yuuki Kaminoh
, et al.
소스
Neurology; 11/25/2014, Vol. 83 Issue 22, p2062-2069, 8p
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