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1 . Academic Journal
Standards of care for CFTR variant-specific therapy (including modulators) for people with cystic fibrosis
저자
by
Southern, Kevin W.
;
Castellani, Carlo
;
Lammertyn, Elise
;
Smyth, Alan
;
VanDevanter, Donald
, et al.
소스
In
Journal of Cystic Fibrosis
January 2023 22(1):17-30
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7 . Academic Journal
Lumacaftor/ivacaftor in people with cystic fibrosis with an A455E–CFTR mutation
저자
by
Berkers, Gitte
;
van der Meer, Renske
;
Heijerman, Harry
;
Beekman, Jeffrey M.
;
Boj, Sylvia F.
, et al.
소스
In
Journal of Cystic Fibrosis
September 2021 20(5):761-767
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7 . Academic Journal
Clinical effects of the three CFTR potentiator treatments curcumin, genistein and ivacaftor in patients with the CFTR-S1251N gating mutation
저자
by
Berkers, Gitte
;
van der Meer, Renske
;
van Mourik, Peter
;
Vonk, Annelotte M
;
Kruisselbrink, Evelien
, et al.
소스
In
Journal of Cystic Fibrosis
November 2020 19(6):955-961
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7 . Academic Journal
Potentiator synergy in rectal organoids carrying S1251N, G551D, or F508del CFTR mutations
저자
by
Dekkers, Johanna F.
;
Van Mourik, Peter
;
Vonk, Annelotte M.
;
Kruisselbrink, Evelien
;
Berkers, Gitte
, et al.
소스
In
Journal of Cystic Fibrosis
September 2016 15(5):568-578
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7 . Academic Journal
R117H-CFTR function and response to VX-770 correlate with mRNA and protein expression in intestinal organoids
저자
by
Van Mourik, Peter
;
van Haaren, Paul
;
Kruisselbrink, Evelien
;
Korkmaz, Cemil
;
Janssens, Hettie M.
, et al.
소스
In
Journal of Cystic Fibrosis
September 2020 19(5):728-732
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7 . Academic Journal
Comparison of Organoid Swelling and Biomarkers of CFTR Function to Determine Effects of Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for the F508del Mutation.
저자
by
Graeber, Simon Y.
;
van Mourik, Peter
;
Vonk, Annelotte M.
;
Kruisselbrink, Evelien
;
Hirtz, Stephanie
, et al.
소스
American Journal of Respiratory & Critical Care Medicine; 12/1/2020, Vol. 202 Issue 11, p1589-1592, 4p
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7 . Academic Journal
Rationale and design of the HIT-CF organoid study: stratifying cystic fibrosis patients based on intestinal organoid response to different CFTR-modulators.
저자
by
van Mourik, Peter
;
Michel, Sabine
;
Vonk, Annelotte M.
;
Beekman, Jeffrey M.
;
van der Ent, Cornelis K.
, et al.
소스
Translational Medicine Communications; 6/3/2020, Vol. 5 Issue 1, p1-8, 8p
Open Access (BioMed Central)
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7 .
Forskolin-induced Organoid Swelling is Associated with Long-term CF Disease Progression
저자
by
Muilwijk, Danya
;
de Poel, Eyleen
;
van Mourik, Peter
;
Suen, Sylvia W F
;
Vonk, Annelotte M
, et al.
소스
European Respiratory Journal, 60(2):2100508, 1-11. EUROPEAN RESPIRATORY SOC JOURNALS LTD
Open Access (OpenAIRE)
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7 . Academic Journal
Comparison of Organoid Swelling and In Vivo Biomarkers of CFTR Function to Determine Effects of Lumacaftor-Ivacaftor in Patients with Cystic Fibrosis Homozygous for the F508del Mutation
저자
by
Graeber, Simon Y.
;
van Mourik, Peter
;
Vonk, Annelotte M.
;
Kruisselbrink, Evelien
;
Hirtz, Stephanie
, et al.
소스
AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE
; DEC 1 2020, 202 11, p1589-p1592, 5p.
Scopus
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7 . Academic Journal
CRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid Biobank
저자
by
Geurts, Maarten H.
;
de Poel, Eyleen
;
Amatngalim, Gimano D.
;
Oka, Rurika
;
Meijers, Fleur M.
, et al.
소스
CELL STEM CELL
; APR 2 2020, 26 4, p503-p+, 15p.
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