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1 . Academic Journal
Screening chimeric GAA variants in preclinical study results in hematopoietic stem cell gene therapy candidate vectors for Pompe disease
저자
by
Dogan, Yildirim
;
Barese, Cecilia N.
;
Schindler, Jeffrey W.
;
Yoon, John K.
;
Unnisa, Zeenath
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
8 December 2022 27:464-487
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7 . Academic Journal
MEIS1 regulates an HLF–oxidative stress axis in MLL-fusion gene leukemia
저자
by
Roychoudhury, Jayeeta
;
Clark, Jason P.
;
Gracia-Maldonado, Gabriel
;
Unnisa, Zeenath
;
Wunderlich, Mark
, et al.
소스
In
Blood
16 April 2015 125(16):2544-2552
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7 . Academic Journal
Meis1 preserves hematopoietic stem cells in mice by limiting oxidative stress
저자
by
Unnisa, Zeenath
;
Clark, Jason P.
;
Roychoudhury, Jayeeta
;
Thomas, Elizabeth
;
Tessarollo, Lino
, et al.
소스
In
Blood
13 December 2012 120(25):4973-4981
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7 . Periodical
High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing
저자
by
Plasschaert, Robert N.
;
DeAndrade, Mark P.
;
Hull, Fritz
;
Nguyen, Quoc
;
Peterson, Tara
, et al.
소스
Molecular Therapy; October 2022, Vol. 30 Issue: 10 p3209-3225, 17p
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7 . Periodical
Preclinical lentiviral vector-mediated hematopoietic stem and progenitor cell gene therapy corrects Pompe disease-related muscle and neurological manifestations
저자
by
Yoon, John K.
;
Schindler, Jeffrey W.
;
Loperfido, Mariana
;
Baricordi, Cristina
;
DeAndrade, Mark P.
, et al.
소스
Molecular Therapy; 20240101, Issue: Preprints
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7 . Academic Journal
MEIS1 Is Required for the Maintenance of Long Term Hematopoietic Stem Cells Wherein It Regulates Quiescence
저자
by
Unnisa, Zeenath
;
Clark, Jason P
;
Wojtowicz, Elizabeth
;
Tessarollo, Lino
;
Copeland, Neal G.
, et al.
소스
In
Blood
18 November 2011 118(21):551-551
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7 . Academic Journal
Aryl Hydrocarbon Receptor Deficiency in an Exon 3 Deletion Mouse Model Promotes Hematopoietic Stem Cell Proliferation and Impacts Endosteal Niche Cells.
저자
by
Unnisa, Zeenath
;
Singh, Kameshwar P.
;
Henry, Ellen C.
;
Donegan, Catherine L.
;
Bennett, John A.
, et al.
소스
Stem Cells International
. 5/30/3016, p1-12. 12p.
Open Access (Wiley)
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7 . Academic Journal
Deficiency in Aryl Hydrocarbon Receptor (AHR) Expression throughout Aging Alters Gene Expression Profiles in Murine Long-Term Hematopoietic Stem Cells.
저자
by
Bennett, John A.
;
Singh, Kameshwar P.
;
Unnisa, Zeenath
;
Welle, Stephen L.
;
Gasiewicz, Thomas A.
.
소스
PLoS ONE
. 7/24/2015, Vol. 10 Issue 7, p1-18. 18p.
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7 . Academic Journal
Gene Therapy Developments for Pompe Disease.
저자
by
Unnisa, Zeenath
;
Yoon, John K.
;
Schindler, Jeffrey W.
;
Mason, Chris
;
van Til, Niek P.
.
소스
Biomedicines; Feb2022, Vol. 10 Issue 2, p302, 1p
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7 . Academic Journal
Long-term hematopoietic stem cell gene therapy corrects neuromuscular manifestations in preclinical study of Pompe mice.
저자
by
van Til, Niek P.
;
Dogan, Yildirim
;
Barese, Cecilia
;
Unnisa, Zeenath
;
Guda, Swaroopa
, et al.
소스
Molecular Genetics & Metabolism
. Feb2021, Vol. 132 Issue 2, pS107-S107. 1p.
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