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1 . Academic Journal
Vosoritide therapy in children with achondroplasia aged 3−59 months: a multinational, randomised, double-blind, placebo-controlled, phase 2 trial
저자
by
Savarirayan, Ravi
;
Wilcox, William R
;
Harmatz, Paul
;
Phillips, John, III
;
Polgreen, Lynda E
, et al.
소스
In
The Lancet Child & Adolescent Health
January 2024 8(1):40-50
Full Text (ScienceDirect)
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7 . Academic Journal
Lifetime impact of achondroplasia: Current evidence and perspectives on the natural history
저자
by
Hoover-Fong, Julie
;
Cheung, Moira S.
;
Fano, Virginia
;
Hagenas, Lars
;
Hecht, Jacqueline T.
, et al.
소스
In
Bone
May 2021 146
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7 . Academic Journal
P141: Persistent growth-promoting effects of vosoritide in children with achondroplasia is accompanied by improvement in physical aspects of quality of life*
저자
by
Savarirayan, Ravi
;
Tofts, Louise
;
Irving, Melita
;
Wilcox, William
;
Bacino, Carlos
, et al.
소스
In
Genetics in Medicine Open
2024 2 Supplement 1
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7 . Academic Journal
P139: Persistent growth-promoting effects of vosoritide in children with achondroplasia for up to 4 years: Update from phase 3 extension study*
저자
by
Savarirayan, Ravi
;
Tofts, Louise
;
Irving, Melita
;
Wilcox, William
;
Bacino, Carlos
, et al.
소스
In
Genetics in Medicine Open
2024 2 Supplement 1
Full Text (ScienceDirect)
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7 . Academic Journal
P131: Persistence of growth-promoting effects in infants and toddlers with achondroplasia: Results from a phase II extension study with vosoritide*
저자
by
Savarirayan, Ravi
;
Wilcox, William
;
Harmatz, Paul
;
Phillips, John, III
;
Polgreen, Lynda
, et al.
소스
In
Genetics in Medicine Open
2024 2 Supplement 1
Full Text (ScienceDirect)
Full Text (Clinical Key)
Full Text (ScienceDirect O/A)
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7 . Academic Journal
Variability of joint hypermobility in children: a meta-analytic approach to set cut-off scores
저자
by
Williams, Cylie M.
;
Welch, James J.
;
Scheper, Mark
;
Tofts, Louise
;
Pacey, Verity
.
소스
European Journal of Pediatrics
. :1-13
Web of Science
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7 . Academic Journal
P193: Persistent growth-promoting effects of vosoritide in children with achondroplasia for up to 3.5 years: Update from phase 3 extension study*
저자
by
Hoover-Fong, Julie
;
Savarirayan, Ravi
;
Tofts, Louise
;
Irving, Melita
;
Wilcox, William
, et al.
소스
In
Genetics in Medicine Open
2023 1(1) Supplement
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Full Text (ScienceDirect O/A)
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7 . Academic Journal
O22: A randomized controlled trial of vosoritide in infants and toddlers with achondroplasia*
저자
by
Bacino, Carlos
;
Savarirayan, Ravi
;
Wilcox, William
;
Harmatz, Paul
;
Phillips, John
, et al.
소스
In
Genetics in Medicine Open
2023 1(1) Supplement
Full Text (ScienceDirect)
Full Text (Clinical Key)
Full Text (ScienceDirect O/A)
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7 . Academic Journal
The Impact of Podiatric Intervention on the Quality of Life and Pain in Children and Adolescents with Hypermobility.
저자
by
Maarj, Muhammad
;
Pacey, Verity
;
Tofts, Louise
;
Clapham, Matthew
;
Coda, Andrea
.
소스
International Journal of Environmental Research & Public Health; Sep2023, Vol. 20 Issue 17, p6623, 13p
Scopus
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7 . Academic Journal
Validation of an Electronic Visual Analog Scale App for Pain Evaluation in Children and Adolescents With Symptomatic Hypermobility: Cross-sectional Study.
저자
by
Maarj, Muhammad
;
Pacey, Verity
;
Tofts, Louise
;
Clapham, Matthew
;
Garcia, Xavier Gironès
, et al.
소스
JMIR Pediatrics & Parenting
. Oct-Dec2022, Vol. 5 Issue 4, p1-9. 9p.
Scopus
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