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1 . Academic Journal
The acute pain crisis in sickle cell disease: What can be done to improve outcomes?
저자
by
Telfer, Paul
;
Anie, Kofi A.
;
Kotsiopoulou, Stella
;
Aiken, Laura
;
Hibbs, Stephen
, et al.
소스
In
Blood Reviews
May 2024 65
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7 . Academic Journal
Haematopoietic stem cell health in sickle cell disease and its implications for stem cell therapies and secondary haematological disorders
저자
by
Gorur, Vishaka
;
Kranc, Kamil R.
;
Ganuza, Miguel
;
Telfer, Paul
.
소스
In
Blood Reviews
January 2024 63
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6 . Academic Journal
The role of haematopoietic stem cell transplantation for sickle cell disease in the era of targeted disease-modifying therapies and gene editing
저자
by
Amrolia, Persis
;
Ansari, Marc
;
Balduzzi, Adriana
;
Dalassier, Arnaud
;
Dalle, Jean-Hugues
, et al.
소스
In
The Lancet Haematology
December 2020 7(12):e902-e911
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7 . Academic Journal
Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial
저자
by
Maggio, Aurelio
;
Kattamis, Antonis
;
Felisi, Mariagrazia
;
Reggiardo, Giorgio
;
El-Beshlawy, Amal
, et al.
소스
In
The Lancet Haematology
June 2020 7(6):e469-e478
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7 . Academic Journal
Efficacy, safety, and pharmacokinetics of a new, ready-to-use, liquid hydroxyurea in children with sickle cell anemia
저자
by
Rankine-Mullings, Angela
;
Keenan, Russell
;
Chakravorty, Subarna
;
Inusa, Baba
;
Telfer, Paul
, et al.
소스
In
Blood Advances
22 August 2023 7(16):4319-4322
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7 . Academic Journal
Deferiprone versus Deferoxamine in Sickle Cell Disease: Results from a 5-year long-term Italian multi-center randomized clinical trial
저자
by
Calvaruso, Giusi
;
Vitrano, Angela
;
Di Maggio, Rosario
;
Ballas, Samir
;
Steinberg, Martin H.
, et al.
소스
In
Blood Cells, Molecules and Diseases
December 2014 53(4):265-271
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7 . Academic Journal
Serial echocardiographic left ventricular ejection fraction measurements: A tool for detecting thalassemia major patients at risk of cardiac death
저자
by
Maggio, Aurelio
;
Vitrano, Angela
;
Calvaruso, Giuseppina
;
Barone, Rita
;
Rigano, Paolo
, et al.
소스
In
Blood Cells, Molecules and Diseases
April 2013 50(4):241-246
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7 . Academic Journal
Elimination of Vaso-Occlusive Crises after Exagamglogene Autotemcel in Patients with Severe Sickle Cell Disease
저자
by
Frangoul, Haydar
;
Locatelli, Franco
;
Sharma, Akshay
;
Bhatia, Monica
;
Mapara, Markus Y.
, et al.
소스
In
Transplantation and Cellular Therapy
February 2024 30(2) Supplement:S234-S235
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7 . Academic Journal
Management of chronic viral hepatitis in patients with thalassemia: recommendations from an international panel
저자
by
Di Marco, Vito
;
Capra, Marcello
;
Angelucci, Emanuele
;
Borgna-Pignatti, Caterina
;
Telfer, Paul
, et al.
소스
In
Blood
21 October 2010 116(16):2875-2883
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7 . Academic Journal
Direct correction of haemoglobin E β-thalassaemia using base editors.
저자
by
Badat, Mohsin
;
Ejaz, Ayesha
;
Hua, Peng
;
Rice, Siobhan
;
Zhang, Weijiao
, et al.
소스
Nature Communications; 4/19/2023, Vol. 14 Issue 1, p1-7, 7p
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