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1 . Academic Journal
Evaluation of a Mobile Phone App for Patients With Pollen-Related Allergic Rhinitis: Prospective Longitudinal Field Study
저자
by
Glattacker, Manuela
;
Boeker, Martin
;
Anger, Robin
;
Reichenbach, Frank
;
Tassoni, Adrian
, et al.
소스
JMIR mHealth and uHealth, Vol 8, Iss 4, p e15514 (2020)
Open Access (DOAJ)
Web of Science
Scopus
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7 . Academic Journal
EURO-NMD registry: federated FAIR infrastructure, innovative technologies and concepts of a patient-centred registry for rare neuromuscular disorders.
저자
by
Atalaia, Antonio
;
Wandrei, Dagmar
;
Lalout, Nawel
;
Thompson, Rachel
;
Tassoni, Adrian
, et al.
소스
Orphanet Journal of Rare Diseases
. 2/14/2024, Vol. 19 Issue 1, p1-15. 15p.
Open Access (BioMed Central)
Web of Science
Scopus
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7 . Academic Journal
Effect of nusinersen on motor, respiratory and bulbar function in early-onset spinal muscular atrophy.
저자
by
Pechmann, Astrid
;
Behrens, Max
;
Dörnbrack, Katharina
;
Tassoni, Adrian
;
Stein, Sabine
, et al.
소스
Brain: A Journal of Neurology
. Feb2023, Vol. 146 Issue 2, p668-677. 10p.
Full Text (OUP)
Web of Science
Scopus
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7 . Academic Journal
Improvements in Walking Distance during Nusinersen Treatment – A Prospective 3-year SMArtCARE Registry Study.
저자
by
Pechmann, Astrid
;
Behrens, Max
;
Dörnbrack, Katharina
;
Tassoni, Adrian
;
Wenzel, Franziska
, et al.
소스
Journal of Neuromuscular Diseases; 2023, Vol. 10 Issue 1, p29-40, 12p
Web of Science
Scopus
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7 . Academic Journal
Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study.
저자
by
Pechmann, Astrid
;
Behrens, Max
;
Dörnbrack, Katharina
;
Tassoni, Adrian
;
Wenzel, Franziska
, et al.
소스
Orphanet Journal of Rare Diseases
. 10/23/2022, Vol. 17 Issue 1, p1-10. 10p.
Open Access (BioMed Central)
Web of Science
Scopus
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7 . Academic Journal
De-duplicating Patient Records from Three Independent Data Sources Reveals the Incidence of Rare Neuromuscular Disorders in Germany.
저자
by
Pechmann, Astrid
;
König, Kirsten
;
Thiele, Simone
;
Walter, Maggie C.
;
Schorling, David
, et al.
소스
Neuropediatrics
. 2019 Supplement2, Vol. 50, pS1-S55. 55p.
Web of Science
Scopus
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7 . Academic Journal
De-duplicating patient records from three independent data sources reveals the incidence of rare neuromuscular disorders in Germany.
저자
by
König, Kirsten
;
Pechmann, Astrid
;
Thiele, Simone
;
Walter, Maggie C.
;
Schorling, David
, et al.
소스
Orphanet Journal of Rare Diseases
. 6/24/2019, Vol. 14 Issue 1, p1-7. 7p.
Open Access (BioMed Central)
Web of Science
Scopus
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7 . Academic Journal
Establishing an Interoperable Clinical Trial Information System ithin MIRACUM.
저자
by
HASSELBLATT, Hanna
;
ANDRAE, Johanna
;
TASSONI, Adrian
;
FITZER, Kai
;
BAHLS, Thomas
, et al.
소스
Studies in Health Technology & Informatics; 2019, Vol. 258, p216-220, 5p, 1 Diagram, 1 Chart
Scopus
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7 .
Cathepsin D as biomarker in cerebrospinal fluid of nusinersen-treated patients with spinal muscular atrophy
저자
by
Schorling, David C.
;
Kölbel, Heike
;
Hentschel, Andreas
;
Pechmann, Astrid
;
Meyer, Nancy
, et al.
소스
Open Access (OpenAIRE)
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7 . Periodical
European Cross-Sectional Survey of Current Care Practices for Duchenne Muscular Dystrophy Reveals Regional and Age-Dependent Differences
저자
by
Vry, Julia
;
Gramsch, Kathrin
;
Rodger, Sunil
;
Thompson, Rachel
;
Steffensen, Birgit F.
, et al.
소스
Journal of Neuromuscular Diseases; November 2016, Vol. 3 Issue: 4 p517-527, 11p
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