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1 . Academic Journal
Transthyretin amyloid cardiomyopathy in France: A cross-sectional multi-centre study (333 patients)
저자
by
Damy, Thibaud
;
Donal, Erwan
;
Lairez, Olivier
;
Eicher, Jean-Christophe
;
Karoubi, Mounira
, et al.
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7 . Academic Journal
Characterization of theory of mind performance in patients with myotonic dystrophy type 1
저자
by
Davion, Jean-Baptiste
;
Tard, Céline
;
Kuchcinski, Grégory
;
Fragoso, Loren
;
Wilu-Wilu, Amina
, et al.
소스
In
Cortex
November 2023 168:181-192
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7 . Academic Journal
The contribution of executive control dysfunction to freezing of gait in Parkinson’s disease
저자
by
Bayot, Madli
;
Dujardin, Kathy
;
Gérard, Morgane
;
Braquet, Aurore
;
Tard, Céline
, et al.
소스
In
Clinical Neurophysiology
August 2023 152:75-89
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7 . Academic Journal
Hypersensitivity infusion-associated reactions induced by enzyme replacement therapy in a cohort of patients with late-onset Pompe disease: An experience from the French Pompe Registry
저자
by
Lessard, Lola E.R.
;
Tard, Céline
;
Salort-Campana, Emmanuelle
;
Sacconi, Sabrina
;
Béhin, Anthony
, et al.
소스
In
Molecular Genetics and Metabolism
July 2023 139(3)
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7 . Academic Journal
Safety and efficacy of zilucoplan in patients with generalised myasthenia gravis (RAISE): a randomised, double-blind, placebo-controlled, phase 3 study
저자
by
Sembinelli, Dylan
;
Teitelbaum, Jeanne
;
Nicolle, Michael
;
Bernard, Emilien
;
Svahn, Juliette
, et al.
소스
In
The Lancet Neurology
May 2023 22(5):395-406
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7 . Academic Journal
Cardiac Outcomes in Adults With Mitochondrial Diseases
저자
by
Savvatis, Konstantinos
;
Vissing, Christoffer Rasmus
;
Klouvi, Lori
;
Florian, Anca
;
Rahman, Mehjabin
, et al.
소스
In
Journal of the American College of Cardiology
11 October 2022 80(15):1421-1430
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7 . Academic Journal
Usage récréatif du protoxyde d’azote : méfaits et mise en garde
저자
by
Deheul, Sylvie
;
Tard, Céline
;
Douillard, Claire
;
Joncquel Chevalier Curt, Marie
;
Azzouz, Ramy
, et al.
소스
In
La Presse Médicale Formation
December 2021 2(6):567-573
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7 . Academic Journal
Safety and efficacy of cipaglucosidase alfa plus miglustat versus alglucosidase alfa plus placebo in late-onset Pompe disease (PROPEL): an international, randomised, double-blind, parallel-group, phase 3 trial
저자
by
Sebok, Agnes
;
Pestronk, Alan
;
Dominovic-Kovacevic, Aleksandra
;
Khan, Aneal
;
Koritnik, Blaž
, et al.
소스
In
The Lancet Neurology
December 2021 20(12):1027-1037
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7 . Academic Journal
Safety and efficacy of avalglucosidase alfa versus alglucosidase alfa in patients with late-onset Pompe disease (COMET): a phase 3, randomised, multicentre trial
저자
by
Behin, Anthony
;
Boentert, Matthias
;
Carvalho, Gerson
;
Chahin, Nizar
;
Charrow, Joel
, et al.
소스
In
The Lancet Neurology
December 2021 20(12):1012-1026
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7 . Academic Journal
Do kinematic gait parameters help to discriminate between fallers and non-fallers with Parkinson’s disease?
저자
by
Delval, Arnaud
;
Betrouni, Nacim
;
Tard, Céline
;
Devos, David
;
Dujardin, Kathy
, et al.
소스
In
Clinical Neurophysiology
February 2021 132(2):536-541
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