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1 . Academic Journal
Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy.
저자
by
Lek, Angela
;
Wong, Brenda
;
Keeler, Allison
;
Blackwood, Meghan
;
Kaiyue Ma
, et al.
소스
New England Journal of Medicine
. 9/28/2023, Vol. 389 Issue 13, p1203-1210. 8p.
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7 . Periodical
PDE10A Inhibition Reduces the Manifestation of Pathology in DMD Zebrafish and Represses the Genetic Modifier PITPNA
저자
by
Lambert, Matthias R.
;
Spinazzola, Janelle M.
;
Widrick, Jeffrey J.
;
Pakula, Anna
;
Conner, James R.
, et al.
소스
Molecular Therapy; March 2021, Vol. 29 Issue: 3 p1086-1101, 16p
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7 . Academic Journal
Repression of phosphatidylinositol transfer protein a ameliorates the pathology of Duchenne muscular dystrophy.
저자
by
Vieira, Natassia M.
;
Spinazzola, Janelle M.
;
Alexander, Matthew S.
;
Moreira, Yuri B.
;
Kawahara, Genri
, et al.
소스
Proceedings of the National Academy of Sciences of the United States of America
. 6/6/2017, Vol. 114 Issue 23, p6080-6085. 6p.
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7 . Academic Journal
Effect of serotonin modulation on dystrophin-deficient zebrafish
저자
by
Spinazzola, Janelle M.
;
Lambert, Matthias R.
;
Gibbs, Devin E.
;
Conner, James R.
;
Krikorian, Georgia L.
, et al.
소스
BIOLOGY OPEN
; AUG 2020, 9 8, pbio053363 8p.
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7 . Periodical
CD82 Is a Marker for Prospective Isolation of Human Muscle Satellite Cells and Is Linked to Muscular Dystrophies
저자
by
Alexander, Matthew S.
;
Rozkalne, Anete
;
Colletta, Alessandro
;
Spinazzola, Janelle M.
;
Johnson, Samuel
, et al.
소스
Cell Stem Cell; December 2016, Vol. 19 Issue: 6 p800-807, 8p
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7 . Academic Journal
Gamma-sarcoglycan is required for the response of archvillin to mechanical stimulation in skeletal muscle
저자
by
Spinazzola, Janelle M.
;
Smith, Tara C.
;
Liu, Min
;
Luna, Elizabeth J.
;
Barton, Elisabeth R.
.
소스
Human Molecular Genetics
. May 01, 2015 24(9):2470-2481
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7 . Academic Journal
Masticatory muscles of mouse do not undergo atrophy in space.
저자
by
Philippou, Anastassios
;
Minozzo, Fabio C.
;
Spinazzola, Janelle M.
;
Smith, Lucas R.
;
Hanqin Lei
, et al.
소스
FASEB Journal
. Jul2015, Vol. 29 Issue 7, p2769-2779. 11p.
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7 . Academic Journal
Mature IGF-I excels in promoting functional muscle recovery from disuse atrophy compared with pro-IGF-IA.
저자
by
SooHyun Park
;
Brisson, Becky K.
;
Min Liu
;
Spinazzola, Janelle M.
;
Barton, Elisabeth R.
.
소스
Journal of Applied Physiology; Apr2014, Vol. 116 Issue 7, p797-806, 10p
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7 . Academic Journal
Automated drug screening with contractile muscle tissue engineered from dystrophic myoblasts.
저자
by
Vandenburgh, Herman
;
Shansky, Janet
;
Benesch-Lee, Frank
;
Skelly, Kirsten
;
Spinazzola, Janelle M.
, et al.
소스
FASEB Journal
. Oct2009, Vol. 23 Issue 10, p3325-3334. 10p. 1 Black and White Photograph, 5 Graphs.
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7 . Periodical
Exosomal Small Talk Carries Strong Messages from Muscle Stem Cells
저자
by
Spinazzola, Janelle M.
;
Gussoni, Emanuela
.
소스
Cell Stem Cell; January 2017, Vol. 20 Issue: 1 p1-3, 3p
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