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1 . Academic Journal
High-throughput screens identify a lipid nanoparticle that preferentially delivers mRNA to human tumors in vivo
저자
by
Huayamares, Sebastian G.
;
Lokugamage, Melissa P.
;
Rab, Regina
;
Da Silva Sanchez, Alejandro J.
;
Kim, Hyejin
, et al.
소스
In
Journal of Controlled Release
May 2023 357:394-403
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7 . Academic Journal
Elexacaftor/VX-445–mediated CFTR interactome remodeling reveals differential correction driven by mutation-specific translational dynamics
저자
by
Kim, Minsoo
;
McDonald, Eli Fritz
;
Sabusap, Carleen Mae P.
;
Timalsina, Bibek
;
Joshi, Disha
, et al.
소스
In
Journal of Biological Chemistry
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7 . Academic Journal
Antisense oligonucleotide-based drug development for Cystic Fibrosis patients carrying the 3849+10 kb C-to-T splicing mutation
저자
by
Oren, Yifat S.
;
Irony-Tur Sinai, Michal
;
Golec, Anita
;
Barchad-Avitzur, Ofra
;
Mutyam, Venkateshwar
, et al.
소스
In
Journal of Cystic Fibrosis
September 2021 20(5):865-875
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7 . Academic Journal
Global assessment of the integrated stress response in CF patient-derived airway and intestinal tissues
저자
by
Bampi, Giovana B.
;
Rauscher, Robert
;
Kirchner, Sebastian
;
Oliver, Kathryn E.
;
Bijvelds, Marcel J.C.
, et al.
소스
In
Journal of Cystic Fibrosis
November 2020 19(6):1021-1026
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7 . Academic Journal
CFTR modulator theratyping: Current status, gaps and future directions
저자
by
Clancy, John Paul
;
Cotton, Calvin U.
;
Donaldson, Scott H.
;
Solomon, George M.
;
VanDevanter, Donald R.
, et al.
소스
In
Journal of Cystic Fibrosis
January 2019 18(1):22-34
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7 . Academic Journal
Relationships between genomic dissipation and de novo SNP evolution.
저자
by
Plyler, Zackery E.
;
McAtee, Christopher W.
;
Hill, Aubrey E.
;
Crowley, Michael R.
;
Tindall, Janice M.
, et al.
소스
PLoS ONE
. 5/16/2024, Vol. 19 Issue 5, p1-14. 14p.
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7 . Periodical
Nucleic acid-based drugs for patients with solid tumours
저자
by
Huayamares, Sebastian G.
;
Loughrey, David
;
Kim, Hyejin
;
Dahlman, James E.
;
Sorscher, Eric J.
.
소스
Nature Reviews Clinical Oncology; June 2024, Vol. 21 Issue: 6 p407-427, 21p
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7 . Book
68 - Fibrosis quística: diagnóstico y tratamiento
저자
by
Solomon, George M.
;
Hoover, Wynton
;
Sorscher, Eric J.
;
Rowe, Steven M.
.
소스
In
Murray y Nadel. Tratado de medicina respiratoria
Edition: Seventh Edition. 2023:919-940
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6 . Book
67 - Fibrosis quística: patogenia y epidemiología
저자
by
Rowe, Steven M.
;
Solomon, George M.
;
Sorscher, Eric J.
.
소스
In
Murray y Nadel. Tratado de medicina respiratoria
Edition: Seventh Edition. 2023:910-918
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5 . Academic Journal
A Novel 7H‑[1,2,4]Triazolo[3,4‑b]thiadiazine-based Cystic Fibrosis Transmembrane Conductance Regulator Potentiator Directed toward Treatment of Cystic Fibrosis.
저자
by
Rab, Andras
;
Yang, Xun
;
Tracy, William F.
;
Hong, Jeong S.
;
Joshi, Disha
, et al.
소스
ACS Medicinal Chemistry Letters; 10/12/2023, Vol. 14 Issue 10, p1338-1343, 6p
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