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1 . Academic Journal
Hematopoietic reconstitution dynamics of mobilized- and bone marrow-derived human hematopoietic stem cells after gene therapy
저자
by
Serena Scala
;
Francesca Ferrua
;
Luca Basso-Ricci
;
Francesca Dionisio
;
Maryam Omrani
, et al.
소스
Nature Communications, Vol 14, Iss 1, Pp 1-18 (2023)
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7 . Academic Journal
S250: UNVEILING THE BIOLOGICAL ROLE OF PERIPHERAL BLOOD HUMAN CIRCULATING HEMATOPOIETIC STEM AND PROGENITOR CELLS
저자
by
Pamela Quaranta
;
Luca Basso-Ricci
;
Raisa Jofra Hernandez
;
Matteo Maria Naldini
;
Matteo Barcella
, et al.
소스
HemaSphere, Vol 7, p e78878d6 (2023)
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7 . Academic Journal
P1392: INTERIM ANALYSIS OF FIRST IN HUMAN PHASE I-II CLINICAL TRIAL OF EX-VIVO GENE THERAPY FOR HURLER SYNDROME: AN UPDATE AT 3 YEAR FOLLOW-UP
저자
by
Francesca Tucci
;
Giulia Consiglieri
;
Chiara Filisetti
;
Maurizio De Pellegrin
;
Renata Mellone
, et al.
소스
HemaSphere, Vol 7, p e1995859 (2023)
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7 . Academic Journal
Wiskott–Aldrich syndrome: Oral findings and microbiota in children and review of the literature
저자
by
Alessandra Lucchese
;
Sabina Cenciarelli
;
Maurizio Manuelli
;
Marta Marcolina
;
Federica Barzaghi
, et al.
소스
Clinical and Experimental Dental Research, Vol 8, Iss 1, Pp 28-36 (2022)
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7 .
Unveiling the Biological Role of Peripheral Blood Human Circulating Hematopoietic Stem and Progenitor Cells
저자
by
Pamela Quaranta
;
Luca Basso-Ricci
;
Raisa Jofra Hernández
;
Matteo Maria Naldini
;
Matteo Barcella
, et al.
소스
Blood
. 140:1977-1978
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7 .
Follicular helper T cell signature of replicative exhaustion, apoptosis, and senescence in common variable immunodeficiency
저자
by
Giulia Milardi
;
Biagio Di Lorenzo
;
Jolanda Gerosa
;
Federica Barzaghi
;
Gigliola Di Matteo
, et al.
소스
European Journal of Immunology (2022). doi:10.1002/eji.202149480
info:cnr-pdr/source/autori:Milardi, Giulia; Di Lorenzo, Biagio; Gerosa, Jolanda; Barzaghi, Federica; Di Matteo, Gigliola; Omrani, Maryam; Jofra, Tatiana; Merelli, Ivan; Barcella, Matteo; Filippini, Matteo; Conti, Anastasia; Ferrua, Francesca; Pozzo Giuffrida, Francesco; Dionisio, Francesca; Rovere-Querini, Patrizia; Marktel, Sarah; Assanelli, Andrea; Piemontese, Simona; Brigida, Immacolata; Zoccolillo, Matteo; Cirillo, Emilia; Giardino, Giuliana; Danieli, Maria Giovanna; Specchia, Fernando; Pacillo, Lucia; Di Cesare, Silvia; Giancotta, Carmela; Romano, Francesca; Matarese, Alessandro; Chetta, Alfredo Antonio; Trimarchi, Matteo; Laurenzi, Andrea; De Pellegrin, Maurizio; Darin, Silvia; Montin, Davide; Marinoni, Maddalena; Dellepiane, Rosa Maria; Sordi, Valeria; Lougaris, Vassilios; Vacca, Angelo; Melzi, Raffaella; Nano, Rita; Azzari, Chiara; Bongiovanni, Lucia; Pignata, Claudio; Cancrini, Caterina; Plebani, Alessandro; Piemonti, Lorenzo; Petrovas, Constantinos; Di Micco, Raffaella; Ponzoni, Maurilio; Aiuti, Alessandro; Cicalese, Maria Pia; Fousteri, Georgia/titolo:Follicular helper T cell signature of replicative exhaustion, apoptosis, and senescence in common variable immunodeficiency/doi:10.1002%2Feji.202149480/rivista:European Journal of Immunology/anno:2022/pagina_da:/pagina_a:/intervallo_pagine:/volume
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7 .
A Novel Assay in Whole Blood Demonstrates Restoration of Mitochondrial Activity in Phagocytes After Successful HSCT in Hyperinflamed X-Linked Chronic Granulomatous Disease
저자
by
Maddalena Migliavacca
;
Luca Basso Ricci
;
Giada Farinelli
;
Valeria Calbi
;
Francesca Tucci
, et al.
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7 .
First-in-human phase I/II clinical trial of hematopoietic stem and progenitor cell gene therapy for Hurler syndrome: Favorable safety profile and extensive metabolic correction
저자
by
Francesca Tucci
;
Bernhard Gentner
;
Stefania Galimberti
;
Francesca Fumagalli
;
Giulia Consiglieri
, et al.
소스
Molecular Genetics and Metabolism
. 135:S121-S122
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7 .
Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapy
저자
by
Maddalena Migliavacca
;
Paola Massariello
;
Roberto Miniero
;
Laura Lorioli
;
Laura Castagnaro
, et al.
소스
Bone marrow transplantation
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7 .
Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis
저자
by
Francesca Ferrua
;
Maria Ester Bernardo
;
Maria Pia Cicalese
;
Francesca Tucci
;
Federica Barzaghi
, et al.
소스
Hepatology (Baltimore, Md.)
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