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1 . Academic Journal
Young mice administered adult doses of AAV5-hFVIII-SQ achieve therapeutic factor VIII expression into adulthood
저자
by
Lening Zhang
;
Bridget Yates
;
Ryan Murphy
;
Su Liu
;
Lin Xie
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 519-531 (2022)
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7 . Academic Journal
Induction of ER Stress by an AAV5 BDD FVIII Construct Is Dependent on the Strength of the Hepatic-Specific Promoter
저자
by
Sylvia Fong
;
Britta Handyside
;
Choong-Ryoul Sihn
;
Su Liu
;
Lening Zhang
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 18, Iss , Pp 620-630 (2020)
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7 . Academic Journal
Prednisolone Does Not Regulate Factor VIII Expression in Mice Receiving AAV5-hFVIII-SQ: Valoctocogene Roxaparvovec
저자
by
Lening Zhang
;
Britta Handyside
;
Ryan Murphy
;
Choong-Ryoul Sihn
;
Lin Xie
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 13-20 (2020)
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7 . Academic Journal
Clearance of Heparan Sulfate and Attenuation of CNS Pathology by Intracerebroventricular BMN 250 in Sanfilippo Type B Mice
저자
by
Mika Aoyagi-Scharber
;
Danielle Crippen-Harmon
;
Roger Lawrence
;
Jon Vincelette
;
Gouri Yogalingam
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 6, Iss C, Pp 43-53 (2017)
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7 . Academic Journal
Pharmacokinetics and biodistribution of a human monoclonal antibody to oxidized LDL in cynomolgus monkey using PET imaging.
저자
by
Amrita V Kamath
;
Simon P Williams
;
Sherry Bullens
;
Kyra J Cowan
;
Yvonne Stenberg
, et al.
소스
PLoS ONE, Vol 7, Iss 9, p e45116 (2012)
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7 .
Vector genome loss and epigenetic modifications mediate decline in transgene expression of AAV5 vectors produced in mammalian and insect cells
저자
by
Britta Handyside
;
Ashrafali Mohamed Ismail
;
Lening Zhang
;
Bridget Yates
;
Lin Xie
, et al.
소스
Molecular Therapy
. 30:3570-3586
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7 .
Intracerebroventricular dosing of N-sulfoglucosamine sulfohydrolase in mucopolysaccharidosis IIIA mice reduces markers of brain lysosomal dysfunction
저자
by
Jenna Magat
;
Samantha Jones
;
Brian Baridon
;
Vishal Agrawal
;
Hio Wong
, et al.
소스
Journal of Biological Chemistry
. 298:102625
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Scopus
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7 .
Induction of ER Stress by an AAV5 BDD FVIII Construct Is Dependent on the Strength of the Hepatic-Specific Promoter
저자
by
Hassib Akeefe
;
Su Liu
;
Jakob Vowinckel
;
Sherry Bullens
;
Choong-Ryoul Sihn
, et al.
소스
Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 18, Iss, Pp 620-630 (2020)
Open Access (OpenAIRE)
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Scopus
JCR 저널정보
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7 .
Prednisolone Does Not Regulate Factor VIII Expression in Mice Receiving AAV5-hFVIII-SQ: Valoctocogene Roxaparvovec
저자
by
Britta Handyside
;
Sílvia Sisó
;
Catherine Vitelli
;
Lening Zhang
;
Danielle Harmon
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 13-20 (2020)
Molecular Therapy. Methods & Clinical Development
Open Access (OpenAIRE)
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7 .
Intracerebroventricular enzyme replacement therapy with β-galactosidase reverses brain pathologies due to GM1 gangliosidosis in mice
저자
by
Alexander Giaramita
;
Nathan Wise
;
Jon Vincelette
;
Rolando De Angelis
;
Brett E. Crawford
, et al.
소스
The Journal of Biological Chemistry
Full Text (ScienceDirect)
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