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1 . Academic Journal
Long-term outcomes after gene therapy for adenosine deaminase severe combined immune deficiency
저자
by
Reinhardt, Bryanna
;
Habib, Omar
;
Shaw, Kit L.
;
Garabedian, Elizabeth
;
Carbonaro-Sarracino, Denise A.
, et al.
소스
In
Blood
14 October 2021 138(15):1304-1316
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7 . Academic Journal
Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy
저자
by
Bradford, Kathryn L.
;
Liu, Siyu
;
Krajinovic, Maja
;
Ansari, Marc
;
Garabedian, Elizabeth
, et al.
소스
In
Biology of Blood and Marrow Transplantation
October 2020 26(10):1819-1827
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7 . Academic Journal
Induction of Fetal Hemoglobin and Reduction of Clinical Manifestations in Patients with Severe Sickle Cell Disease Treated with Shmir-Based Lentiviral Gene Therapy for Post-Transcriptional Gene Editing of BCL11A: Updated Results from Pilot and Feasibility Trial
저자
by
Esrick, Erica B.
;
Federico, Amy
;
Abriss, Daniela
;
Armant, Myriam
;
Boardman, Kari
, et al.
소스
In
Blood
15 November 2022 140 Supplement 1:10665-10667
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7 . Academic Journal
Gene therapy for adenosine deaminase–deficient severe combined immune deficiency: clinical comparison of retroviral vectors and treatment plans
저자
by
Candotti, Fabio
;
Shaw, Kit L.
;
Muul, Linda
;
Carbonaro, Denise
;
Sokolic, Robert
, et al.
소스
In
Blood
1 November 2012 120(18):3635-3646
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7 . Academic Journal
Phase I Study of PHE885, a Fully Human BCMA-Directed CAR-T Cell Therapy for Relapsed/Refractory Multiple Myeloma Manufactured in
저자
by
Sperling, Adam S.
;
Nikiforow, Sarah
;
Nadeem, Omar
;
Mo, Clifton C
;
Laubach, Jacob P.
, et al.
소스
In
Blood
23 November 2021 138 Supplement 1:3864-3864
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7 . Academic Journal
Lentiviral Gene Therapy with Autologous Hematopoietic Stem and Progenitor Cells (HSPCs) for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency (ADA-SCID): Results in an Expanded Cohort
저자
by
Kohn, Donald B.
;
Shaw, Kit L.
;
Garabedian, Elizabeth
;
Carbonaro-Sarracino, Denise Ann
;
Moore, Theodore B.
, et al.
소스
In
Blood
13 November 2019 134 Supplement 1:3345-3345
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7 . Periodical
Lentiviral gene therapy for X-linked chronic granulomatous disease
저자
by
Kohn, Donald B.
;
Booth, Claire
;
Kang, Elizabeth M.
;
Pai, Sung-Yun
;
Shaw, Kit L.
, et al.
소스
Nature Medicine; February 2020, Vol. 26 Issue: 2 p200-206, 7p
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7 . Academic Journal
Autologous Transplant/Gene Therapy for Adenosine Deaminase-Deficient Severe Combined Immune Deficiency
저자
by
Kohn, Donald B.
;
Shaw, Kit L.
;
Sokolic, Robert
;
Carbonaro, Denise A.
;
Davila, Alejandar
, et al.
소스
In
Biology of Blood and Marrow Transplantation
February 2015 21(2) Supplement:S102-S102
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7 . Academic Journal
Clinical efficacy of gene-modified stem cells in adenosine deaminase-deficient immunodeficiency.
저자
by
Shaw, Kit L.
;
Garabedian, Elizabeth
;
Mishra, Suparna
;
Barman, Provaboti
;
Davila, Alejandra
, et al.
소스
Journal of Clinical Investigation
. May2017, Vol. 127 Issue 5, p1689-1699. 11p. 1 Diagram, 3 Charts, 4 Graphs.
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7 . Academic Journal
A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency
저자
by
Hacein-Bey-Abina, Salima
;
Pai, Sung-Yun
;
Gaspar, Bobby H.
;
Armant, Myriam
;
Berry, Charles C.
, et al.
소스
The New England Journal of Medicine
. Oct 09, 2014 371(15):1407-1417
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