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1 . Academic Journal
In vivo targeted delivery of nucleic acids and CRISPR genome editors enabled by GSH-responsive silica nanoparticles
저자
by
Wang, Yuyuan
;
Shahi, Pawan K.
;
Wang, Xiuxiu
;
Xie, Ruosen
;
Zhao, Yi
, et al.
소스
In
Journal of Controlled Release
10 August 2021 336:296-309
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7 . Academic Journal
A pH-responsive silica–metal–organic framework hybrid nanoparticle for the delivery of hydrophilic drugs, nucleic acids, and CRISPR-Cas9 genome-editing machineries
저자
by
Wang, Yuyuan
;
Shahi, Pawan K.
;
Xie, Ruosen
;
Zhang, Huilong
;
Abdeen, Amr A.
, et al.
소스
In
Journal of Controlled Release
10 August 2020 324:194-203
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7 . Academic Journal
Nonviral base editing of KCNJ13 mutation preserves vision in a model of inherited retinal channelopathy.
저자
by
Kabra, Meha
;
Shahi, Pawan K.
;
Yuyuan Wang
;
Sinha, Divya
;
Spillane, Allison
, et al.
소스
Journal of Clinical Investigation
. 10/2/2023, Vol. 133 Issue 19, p1-15. 15p.
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7 . Academic Journal
Kir7.1 disease mutant T153I within the inner pore affects K
+
conduction.
저자
by
Beverley, Katie M.
;
Shahi, Pawan K.
;
Kabra, Meha
;
Qianqian Zhao
;
Heyrman, Joseph
, et al.
소스
American Journal of Physiology: Cell Physiology
. Jul2022, Vol. 323 Issue 1, pC56-C68. 13p.
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7 . Academic Journal
A mutation in transmembrane protein 135 impairs lipid metabolism in mouse eyecups.
저자
by
Landowski, Michael
;
Bhute, Vijesh J.
;
Takimoto, Tetsuya
;
Grindel, Samuel
;
Shahi, Pawan K.
, et al.
소스
Scientific Reports
. 1/14/2022, Vol. 12 Issue 1, p1-14. 14p.
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7 . Academic Journal
Hypoxic–ischemic injury causes functional and structural neurovascular degeneration in the juvenile mouse retina.
저자
by
Zaitoun, Ismail S.
;
Shahi, Pawan K.
;
Suscha, Andrew
;
Chan, Kore
;
McLellan, Gillian J.
, et al.
소스
Scientific Reports
. 6/16/2021, Vol. 11 Issue 1, p1-13. 13p.
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7 . Academic Journal
Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy.
저자
by
Sinha, Divya
;
Steyer, Benjamin
;
Shahi, Pawan K.
;
Mueller, Katherine P.
;
Valiauga, Rasa
, et al.
소스
American Journal of Human Genetics
. Aug2020, Vol. 107 Issue 2, p278-292. 15p.
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7 . Periodical
A biodegradable nanocapsule delivers a Cas9 ribonucleoprotein complex for in vivo genome editing
저자
by
Chen, Guojun
;
Abdeen, Amr A.
;
Wang, Yuyuan
;
Shahi, Pawan K.
;
Robertson, Samantha
, et al.
소스
Nature Nanotechnology; October 2019, Vol. 14 Issue: 10 p974-980, 7p
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7 . Academic Journal
Gene Augmentation and Readthrough Rescue Channelopathy in an iPSC-RPE Model of Congenital Blindness.
저자
by
Shahi, Pawan K.
;
Hermans, Dalton
;
Sinha, Divya
;
Brar, Simran
;
Moulton, Hannah
, et al.
소스
American Journal of Human Genetics
. Feb2019, Vol. 104 Issue 2, p310-318. 9p.
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7 . Academic Journal
Role of the sigma-1 receptor chaperone in rod and cone photoreceptor degenerations in a mouse model of retinitis pigmentosa.
저자
by
Huan Yang
;
Yingmei Fu
;
Xinying Liu
;
Shahi, Pawan K.
;
Mavlyutov, Timur A.
, et al.
소스
Molecular Neurodegeneration
. 9/19/2017, Vol. 12, p1-15. 15p. 2 Diagrams, 8 Graphs.
Open Access (BioMed Central)
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