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1 . Academic Journal
Screening chimeric GAA variants in preclinical study results in hematopoietic stem cell gene therapy candidate vectors for Pompe disease
저자
by
Dogan, Yildirim
;
Barese, Cecilia N.
;
Schindler, Jeffrey W.
;
Yoon, John K.
;
Unnisa, Zeenath
, et al.
소스
In
Molecular Therapy - Methods & Clinical Development
8 December 2022 27:464-487
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7 . Periodical
High-throughput analysis of hematopoietic stem cell engraftment after intravenous and intracerebroventricular dosing
저자
by
Plasschaert, Robert N.
;
DeAndrade, Mark P.
;
Hull, Fritz
;
Nguyen, Quoc
;
Peterson, Tara
, et al.
소스
Molecular Therapy; October 2022, Vol. 30 Issue: 10 p3209-3225, 17p
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7 . Periodical
Preclinical lentiviral vector-mediated hematopoietic stem and progenitor cell gene therapy corrects Pompe disease-related muscle and neurological manifestations
저자
by
Yoon, John K.
;
Schindler, Jeffrey W.
;
Loperfido, Mariana
;
Baricordi, Cristina
;
DeAndrade, Mark P.
, et al.
소스
Molecular Therapy; 20240101, Issue: Preprints
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7 . Periodical
Inducible histone K-to-M mutations are dynamic tools to probe the physiological role of site-specific histone methylation in vitro and in vivo
저자
by
Brumbaugh, Justin
;
Kim, Ik Soo
;
Ji, Fei
;
Huebner, Aaron J.
;
Di Stefano, Bruno
, et al.
소스
Nature Cell Biology; November 2019, Vol. 21 Issue: 11 p1449-1461, 13p
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7 . Academic Journal
Gene Therapy Developments for Pompe Disease.
저자
by
Unnisa, Zeenath
;
Yoon, John K.
;
Schindler, Jeffrey W.
;
Mason, Chris
;
van Til, Niek P.
.
소스
Biomedicines; Feb2022, Vol. 10 Issue 2, p302, 1p
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7 . Academic Journal
Gfi-1 restricts proliferation and preserves functional integrity of haematopoietic stem cells.
저자
by
Hock, Hanno
;
Hamblen, Melanie J.
;
Rooke, Heather M.
;
Schindler, Jeffrey W.
;
Saleque, Shireen
, et al.
소스
Nature
. 10/21/2004, Vol. 431 Issue 7011, p1002-1007. 6p.
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7 . Academic Journal
Tel/Etv6 is an essential and selective regulator of adult hematopoietic stem cell survival.
저자
by
Hock, Hanno
;
Meade, Eliza
;
Medeiros, Sarah
;
Schindler, Jeffrey W.
;
Valk, Peter J. M.
, et al.
소스
Genes & Development
. 10/1/2004, Vol. 18 Issue 19, p2336-2341. 7p. 4 Diagrams.
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7 . Academic Journal
The Hippo pathway target, YAP, promotes metastasis through its TEAD-interaction domain
저자
by
Lamar, John M.
;
Stern, Patrick
;
Liu, Hui
;
Schindler, Jeffrey W.
;
Jiang, Zhi-Gang
, et al.
소스
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA
; SEP 11 2012, 109 37, pE2441-pE2450, 10p.
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7 . Academic Journal
TEL-AML1 Corrupts Hematopoietic Stem Cells to Persist in the Bone Marrow and Initiate Leukemia
저자
by
Schindler, Jeffrey W.
;
Van Buren, Denille
;
Foudi, Adlen
;
Krejci, Ondrej
;
Qin, Jinzhong
, et al.
소스
CELL STEM CELL
; JUL 2 2009, 5 1, p43-p53, 11p.
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7 . Academic Journal
Analysis of histone 2B-GFP retention reveals slowly cycling hematopoietic stem cells
저자
by
Foudi, Adlen
;
Hochedlinger, Konrad
;
Van Buren, Denille
;
Schindler, Jeffrey W.
;
Jaenisch, Rudolf
, et al.
소스
NATURE BIOTECHNOLOGY
; JAN 2009, 27 1, p84-p90, 7p.
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