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1 . Academic Journal
SERCA2a overexpression improves muscle function in a canine Duchenne muscular dystrophy model
저자
by
Kasun Kodippili
;
Chady H. Hakim
;
Matthew J. Burke
;
Yongping Yue
;
James A. Teixeira
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 2, Pp 101268- (2024)
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7 . Academic Journal
Thorough molecular configuration analysis of noncanonical AAV genomes in AAV vector preparations
저자
by
Junping Zhang
;
Xiangping Yu
;
Matthew Chrzanowski
;
Jiahe Tian
;
Derek Pouchnik
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101215- (2024)
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7 . Academic Journal
B cell focused transient immune suppression protocol for efficient AAV readministration to the liver
저자
by
Jyoti Rana
;
Roland W. Herzog
;
Maite Muñoz-Melero
;
Kentaro Yamada
;
Sandeep R.P. Kumar
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101216- (2024)
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7 . Academic Journal
A novel class of self-complementary AAV vectors with multiple advantages based on cceAAV lacking mutant ITR
저자
by
Junping Zhang
;
Dylan A. Frabutt
;
Matthew Chrzanowski
;
Ning Li
;
Lohra M. Miller
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 32, Iss 1, Pp 101206- (2024)
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7 . Academic Journal
Quantitative analysis of preferential utilization of AAV ITR as the packaging terminal signal
저자
by
Xin Li
;
Lohra Mickelle Miller
;
Matthew Chrzanowski
;
Jiahe Tian
;
Martin F. Jarrold
, et al.
소스
Frontiers in Bioengineering and Biotechnology, Vol 11 (2023)
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7 . Academic Journal
Distinct functions and transcriptional signatures in orally induced regulatory T cell populations
저자
by
Moanaro Biswas
;
Kaman So
;
Thais B. Bertolini
;
Preethi Krishnan
;
Jyoti Rana
, et al.
소스
Frontiers in Immunology, Vol 14 (2023)
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7 . Academic Journal
Liver-specific in vivo base editing of Angptl3 via AAV delivery efficiently lowers blood lipid levels in mice
저자
by
Yuanbojiao Zuo
;
Chen Zhang
;
Yuan Zhou
;
Haiwen Li
;
Weidong Xiao
, et al.
소스
Cell & Bioscience, Vol 13, Iss 1, Pp 1-9 (2023)
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7 . Academic Journal
Chemical modification of AAV9 capsid with N-ethyl maleimide alters vector tissue tropism
저자
by
Patrick L. Mulcrone
;
Anh K. Lam
;
Dylan Frabutt
;
Junping Zhang
;
Matthew Chrzanowski
, et al.
소스
Scientific Reports, Vol 13, Iss 1, Pp 1-14 (2023)
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7 . Academic Journal
Adding recombinant AAVs to the cancer therapeutics mix
저자
by
Patrick L. Mulcrone
;
Roland W. Herzog
;
Weidong Xiao
.
소스
Molecular Therapy: Oncolytics, Vol 27, Iss , Pp 73-88 (2022)
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5 . Academic Journal
Fast and high-throughput LC-MS characterization, and peptide mapping of engineered AAV capsids using LC-MS/MS
저자
by
Anh K. Lam
;
Junping Zhang
;
Dylan Frabutt
;
Patrick L. Mulcrone
;
Lei Li
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 27, Iss , Pp 185-194 (2022)
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