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1 . Academic Journal
Interim analysis: Open-label extension study of leniolisib for patients with APDS
저자
by
Rao, V. Koneti
;
Kulm, Elaine
;
Šedivá, Anna
;
Plebani, Alessandro
;
Schuetz, Catharina
, et al.
소스
In
The Journal of Allergy and Clinical Immunology
January 2024 153(1):265-274
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7 . Academic Journal
A randomized, placebo-controlled phase 3 trial of the PI3Kδ inhibitor leniolisib for activated PI3Kδ syndrome
저자
by
Rao, V. Koneti
;
Webster, Sharon
;
Šedivá, Anna
;
Plebani, Alessandro
;
Schuetz, Catharina
, et al.
소스
In
Blood
2 March 2023 141(9):971-983
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7 . Academic Journal
Population pharmacokinetics of recombinant human C1 esterase inhibitor in children with hereditary angioedema
저자
by
Hayes, Siobhán
;
Farrell, Colm
;
Relan, Anurag
;
Anderson, John
.
소스
In
Annals of Allergy, Asthma & Immunology
June 2021 126(6):707-712
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6 . Academic Journal
Recombinant human C1 esterase inhibitor for hereditary angioedema attacks: A European registry
저자
by
Valerieva, Anna
;
Staevska, Maria T.
;
Grivcheva-Panovska, Vesna
;
Jesenak, Milos
;
Kőhalmi, Kinga Viktória
, et al.
소스
In
World Allergy Organization Journal
April 2021 14(4)
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7 . Academic Journal
63 Clinical Roadmap for Implementing Results from Electronic Health Records Queries
저자
by
FitzPatrick, Amy
;
Cunningham-Rundles, Charlotte
;
Sacco, Keith
;
Chin, Aaron
;
Butte, Manish
, et al.
소스
In
Clinical Immunology
May 2024 262 Supplement
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7 . Academic Journal
32 Clinical and Genetic Findings of >5,300 Individuals Tested via the navigateAPDS Sponsored Genetic Testing Program
저자
by
Campbell, Emily
;
Park, Nami
;
Morales, Ana
;
Hartline, Brian
;
Relan, Anurag
, et al.
소스
In
Clinical Immunology
May 2024 262 Supplement
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7 . Academic Journal
Recombinant human C1 esterase inhibitor for prophylaxis of hereditary angio-oedema: a phase 2, multicentre, randomised, double-blind, placebo-controlled crossover trial
저자
by
Riedl, Marc A
;
Grivcheva-Panovska, Vesna
;
Moldovan, Dumitru
;
Baker, James
;
Yang, William H
, et al.
소스
In
The Lancet
30 September-6 October 2017 390(10102):1595-1602
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7 . Academic Journal
P633: Clinical and genetic findings of >3,900 individuals tested via the navigateAPDS sponsored genetic testing program
저자
by
McLaughlin, Heather
;
Campbell, Emily
;
Park, Nami
;
Morales, Ana
;
Hartline, Brian
, et al.
소스
In
Genetics in Medicine Open
2024 2 Supplement 1
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7 . Academic Journal
Recombinant Human C1-Esterase Inhibitor to Treat Acute Hereditary Angioedema Attacks in Adolescents
저자
by
Baker, James W.
;
Reshef, Avner
;
Moldovan, Dumitru
;
Harper, Joseph R.
;
Relan, Anurag
, et al.
소스
In
The Journal of Allergy and Clinical Immunology: In Practice
July-August 2017 5(4):1091-1097
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7 . Academic Journal
Sustained response of recombinant human C1 esterase inhibitor for acute treatment of hereditary angioedema attacks
저자
by
Bernstein, Jonathan A.
;
Relan, Anurag
;
Harper, Joseph R.
;
Riedl, Marc
.
소스
In
Annals of Allergy, Asthma & Immunology
April 2017 118(4):452-455
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