Dipòsit Digital de Documents de la UAB Universitat Autònoma de Barcelona BASE-Bielefeld Academic Search Engine Molecular Therapy. Methods & Clinical Development Molecular Therapy-Methods and Clinical Development, 8, 152-165. Cell Press Yadak, R, Cabrera-Pérez, R, Torres-Torronteras, J, Bugiani, M, Haeck, J C, Huston, M W, Bogaerts, E, Goffart, S, Jacobs, E H, Stok, M, Leonardelli, L, Biasco, L, Verdijk, R M, Bernsen, M R, Ruijter, G, Martí, R, Wagemaker, G, van Til, N P & de Coo, I F M 2018, ' Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE ', Molecular Therapy-Methods and Clinical Development, vol. 8, pp. 152-165 . https://doi.org/10.1016/j.omtm.2018.01.001 Molecular Therapy-Methods & Clinical Development, 8, 152-165. Cell Press Molecular Therapy: Methods & Clinical Development, Vol 8, Iss C, Pp 152-165 (2018)