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1 . Academic Journal
Unveiling the untreated: development of a database algorithm to identify potential Fabry disease patients in Germany
저자
by
Max J. Hilz
;
Nicole Lyn
;
Felix Marczykowski
;
Barbara Werner
;
Marc Pignot
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 19, Iss 1, Pp 1-11 (2024)
Open Access (BioMed Central)
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7 . Academic Journal
Differential humanistic and economic burden of mild, moderate and severe haemophilia in european adults: a regression analysis of the CHESS II study
저자
by
Idaira Rodriguez-Santana
;
Pronabesh DasMahapatra
;
Tom Burke
;
Zalmai Hakimi
;
José Bartelt-Hofer
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-10 (2022)
Open Access (BioMed Central)
Open Access (DOAJ)
Web of Science
Scopus
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7 . Academic Journal
Health-related quality of life, direct medical and societal costs among children with moderate or severe haemophilia in Europe: multivariable models of the CHESS-PAEDs study
저자
by
Idaira Rodriguez-Santana
;
Pronabesh DasMahapatra
;
Tom Burke
;
Zalmai Hakimi
;
José Bartelt-Hofer
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 17, Iss 1, Pp 1-9 (2022)
Open Access (BioMed Central)
Open Access (DOAJ)
Web of Science
Scopus
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7 . Academic Journal
Development of the Fabry Disease Patient-Reported Outcome (FD-PRO): a new instrument to measure the symptoms and impacts of Fabry Disease
저자
by
Alaa Hamed
;
Pronabesh DasMahapatra
;
Nicole Lyn
;
Chad Gwaltney
;
Robert J. Hopkin
.
소스
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-12 (2021)
Open Access (BioMed Central)
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7 . Academic Journal
Fabry Disease Patient-Reported Outcome (FD-PRO) demonstrates robust measurement properties for assessing symptom severity in Fabry disease
저자
by
Alaa Hamed
;
Pronabesh DasMahapatra
;
Nicole Lyn
;
Chad Gwaltney
;
Charlie Iaconangelo
, et al.
소스
Molecular Genetics and Metabolism Reports, Vol 29, Iss , Pp 100824- (2021)
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7 . Academic Journal
In search of a daily physical activity 'sweet spot': Piloting a digital tracking intervention for people with multiple sclerosis
저자
by
Emil Chiauzzi
;
Eric B Hekler
;
Jisoo Lee
;
Auriell Towner
;
Pronabesh DasMahapatra
, et al.
소스
Digital Health, Vol 5 (2019)
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7 .
Cost-Effectiveness Analysis of rFVIIIFc Versus Contemporary rFVIII Treatments for Patients with Severe Hemophilia A Without Inhibitors in the United States
저자
by
Ron Preblick
;
Talaha Ali
;
Emma S Knowles
;
Ash Bullement
;
Pronabesh DasMahapatra
.
소스
PharmacoEconomics Open
Open Access (OpenAIRE)
Web of Science
Scopus
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RefWorks
7 .
Development of the Fabry Disease Patient-Reported Outcome (FD-PRO): a new instrument to measure the symptoms and impacts of Fabry Disease
저자
by
Chad Gwaltney
;
Alaa Hamed
;
Pronabesh DasMahapatra
;
Nicole Lyn
;
Robert J. Hopkin
.
소스
Orphanet Journal of Rare Diseases, Vol 16, Iss 1, Pp 1-12 (2021)
Orphanet Journal of Rare Diseases
Open Access (BioMed Central)
Open Access (OpenAIRE)
Web of Science
Scopus
JCR 저널정보
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7 .
Fitusiran Reaches People's with Hemophilia and Their Caregivers’ Treatment Expectations: Qualitative Semi-Structured Interviews of Participants of ATLAS-OLE Trial (Interim analysis)
저자
by
Alok Srivastava
;
Savita Rangarajan
;
Cecil Ross
;
Christina Slota
;
Dana DiBenedetti
, et al.
소스
Blood
. 140:7989-7990
Full Text (ScienceDirect O/A)
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7 .
Patients with Hemophilia and Their Caregivers Prefer Treatment Attributes That Enable a More Active Lifestyle with Lower Risk of Inhibitor Development
저자
by
Viridiana Cano
;
Carol Mansfield
;
Anna Pierce
;
Colton Leach
;
Jane Cavanaugh Smith
, et al.
소스
Blood
. 140:7991-7992
Full Text (ScienceDirect O/A)
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