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1 . Academic Journal
Achieving access to haemophilia care in low-income and lower-middle-income countries: expanded Humanitarian Aid Program of the World Federation of Hemophilia after 5 years
저자
by
Pierce, Glenn F
;
Adediran, Megan
;
Diop, Saliou
;
Dunn, Amy L
;
El Ekiaby, Magdy
, et al.
소스
In
The Lancet Haematology
September 2022 9(9):e689-e697
Full Text (ScienceDirect)
Full Text (Clinical Key)
Web of Science
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7 . Academic Journal
Risk of harm to people with haemophilia from the 2023 WHO Essential Medicines List
저자
by
Crato, Miguel
;
Dunn, Amy
;
Gouider, Emna
;
Mahlangu, Johnny
;
Page, David
, et al.
소스
In
The Lancet Haematology
September 2024 11(9):e638-e640
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7 . Academic Journal
Recombinant factor IX Fc fusion protein in children with haemophilia B (Kids B-LONG): results from a multicentre, non-randomised phase 3 study
저자
by
Fischer, Kathelijn
;
Kulkarni, Roshni
;
Nolan, Beatrice
;
Mahlangu, Johnny
;
Rangarajan, Savita
, et al.
소스
In
The Lancet Haematology
February 2017 4(2):e75-e82
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7 . Periodical
Risk of harm to people with haemophilia from the 2023 WHO Essential Medicines List
저자
by
Pierce, Glenn F
;
O'Mahony, Brian
;
Kaczmarek, Radoslaw
;
Skinner, Mark W
;
Makris, Mike
, et al.
소스
The Lancet Haematology; September 2024, Vol. 11 Issue: 9 pe638-e640, 3p
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7 . Academic Journal
Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia A.
저자
by
Pasi, K John
;
Laffan, Michael
;
Rangarajan, Savita
;
Robinson, Tara M
;
Mitchell, Nina
, et al.
소스
Haemophilia
. Nov2021, Vol. 27 Issue 6, p947-956. 10p. 1 Chart, 5 Graphs.
Web of Science
Scopus
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7 .
Towards achieving a haemophilia-free mind
저자
by
Hermans, Cédric
;
Pierce, Glenn F
;
UCL - SSS/IREC/CARD - Pôle de recherche cardiovasculaire
;
UCL - (SLuc) Service d'hématologie
;
UCL - (SLuc) Centre de malformations vasculaires congénitales
.
소스
Haemophilia, p. [1-3] (2023)
Open Access (OpenAIRE)
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7 . Academic Journal
Clinical Outcomes in Children with Hemophilia B Treated Long Term with rFIXFc: Interim Results of the B-YOND Extension Study
저자
by
Kulkarni, Roshni
;
Nolan, Beatrice
;
Bennett, Carolyn M.
;
Fischer, Kathelijn
;
Perry, David J
, et al.
소스
In
Blood
3 December 2015 126(23):1093-1093
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7 . Academic Journal
Extended-Interval Prophylaxis with rFIXFc in Adults and Adolescents with Hemophilia B: Interim Results of the B-YOND Extension Study
저자
by
Mahlangu, Johnny
;
Shapiro, Amy D
;
Pasi, K John
;
Ragni, Margaret V
;
Ozelo, Margareth Castro
, et al.
소스
In
Blood
3 December 2015 126(23):1088-1088
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7 . Academic Journal
Long-Term Safety and Efficacy of rFVIIIFc in Adults and Adolescents with Severe Hemophilia A: A Longitudinal Analysis of A-LONG and ASPIRE
저자
by
Pasi, K John
;
Perry, David J
;
Mahlangu, Johnny
;
Konkle, Barbara A
;
Rangarajan, Savita
, et al.
소스
In
Blood
3 December 2015 126(23):1087-1087
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7 . Academic Journal
Predicting FIX Activity in Prophylaxis Patients Using Recombinant FIX Fc Fusion Protein for Treatment of Bleeding Episodes
저자
by
Powell, Jerry S
;
Ozelo, Margareth
;
Ragni, Margaret V.
;
Pasi, John
;
Perry, David J.
, et al.
소스
In
Blood
6 December 2014 124(21):2842-2842
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