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1 . Academic Journal
Inhibition of the alternative complement pathway by antisense oligonucleotides targeting complement factor B improves lupus nephritis in mice
저자
by
Grossman, Tamar R.
;
Hettrick, Lisa A.
;
Johnson, Robert B.
;
Hung, Gene
;
Peralta, Raechel
, et al.
소스
In
Immunobiology
June 2016 221(6):701-708
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7 . Academic Journal
Targeting KLF1 for the Treatment of Sickle Cell Disease Using Antisense Oligonucleotides
저자
by
Peralta, Raechel
;
Low, Audrey
;
Booten, Sheri
;
Zhou, Dewang
;
Kim, Aneeza
, et al.
소스
In
Blood
6 December 2014 124(21):4038-4038
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7 . Academic Journal
Cardiovascular and Metabolic Effects of ANGPTL3 Antisense Oligonucleotides.
저자
by
Graham, Mark J.
;
Lee, Richard G.
;
Brandt, Teresa A.
;
Li-Jung Tai
;
Wuxia Fu
, et al.
소스
New England Journal of Medicine
. 7/20/2017, Vol. 377 Issue 3, p222-232. 11p.
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7 . Book
Knockdown of Nuclear-Retained Long Noncoding RNAs Using Modified DNA Antisense Oligonucleotides.
저자
by
Zong, Xinying
;
Huang, Lulu
;
Tripathi, Vidisha
;
Peralta, Raechel
;
Freier, Susan M.
, et al.
소스
Nuclear Bodies & Noncoding RNAs; 2015, p321-331, 11p
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7 . Academic Journal
Peripheral Androgen Receptor Gene Suppression Rescues Disease in Mouse Models of Spinal and Bulbar Muscular Atrophy.
저자
by
Lieberman, Andrew P.
;
Yu, Zhigang
;
Murray, Sue
;
Peralta, Raechel
;
Low, Audrey
, et al.
소스
Cell Reports; May2014, Vol. 7 Issue 3, p774-784, 11p
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7 . Academic Journal
Characterization of Target mRNA Reduction Through In Situ RNA Hybridization in Multiple Organ Systems Following Systemic Antisense Treatment in Animals.
저자
by
Hung, Gene
;
Xiao, Xiaokun
;
Peralta, Raechel
;
Bhattacharjee, Gourab
;
Murray, Sue
, et al.
소스
Nucleic Acid Therapeutics
. Dec2013, Vol. 23 Issue 6, p369-378. 10p.
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7 . Academic Journal
Reducing TMPRSS6 ameliorates hemochromatosis and β-thalassemia in mice
저자
by
Guo, Shuling
;
Casu, Carla
;
Gardenghi, Sara
;
Booten, Sheri
;
Aghajan, Mariam
, et al.
소스
Journal of Clinical Investigation
. Apr 01, 2013 123(4):1531-1541
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7 . Academic Journal
Reducing TMPRSS6 ameliorates hemochromatosis and β-thalassemia in mice.
저자
by
Shuling Guo
;
Casu, Carla
;
Gardenghi, Sara
;
Booten, Sheri
;
Aghajan, Mariam
, et al.
소스
Journal of Clinical Investigation
. Apr2013, Vol. 123 Issue 4, p1531-1541. 11p. 1 Diagram, 5 Graphs.
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7 . Periodical
Unique O-Methoxyethyl Ribose-DNA Chimeric Oligonucleotide Induces an Atypical Melanoma Differentiation-Associated Gene 5-Dependent Induction of Type I Interferon Response.
저자
by
Burel, Sebastien A
;
Machemer, Todd
;
Ragone, Frank L
;
Kato, Hiroki
;
Cauntay, Patrick
, et al.
소스
The Journal of Pharmacology and Experimental Therapeutics; July 2012, Vol. 342 Issue: 1 p150-162, 13p
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7 . Academic Journal
Adult Hemoglobin Production, Chain Rebalance, and Splice Correction in IVS2-745 Beta-Thalassemia Patient Cells Using 2'-O-Methoxyethyl Splice-Switching Oligos
저자
by
Dong, Alisa Cheung
;
Ghiaccio, Valentina
;
Motta, Irene
;
Guo, Shuling
;
Peralta, Raechel
, et al.
소스
BLOOD
; DEC 2 2016, 128 22, 6p.
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