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1 . Academic Journal
Progress and harmonization of gene editing to treat human diseases: Proceeding of COST Action CA21113 GenE-HumDi
저자
by
Alessia Cavazza
;
Ayal Hendel
;
Rasmus O. Bak
;
Paula Rio
;
Marc Güell
, et al.
소스
Molecular Therapy: Nucleic Acids, Vol 34, Iss , Pp 102066- (2023)
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7 . Academic Journal
S256: HLA-E/NKG2A CHECKPOINT DRIVES MULTIPLE MYELOMA RESISTANCE TO CAR-NK THERAPY
저자
by
Jessica Encinas
;
Almudena García-Ortiz
;
Elena Maroto-Martín
;
Eva Castellano
;
Raquel Oliva
, et al.
소스
HemaSphere, Vol 7, p e16745e9 (2023)
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7 . Academic Journal
Adenine base editing efficiently restores the function of Fanconi anemia hematopoietic stem and progenitor cells
저자
by
Sebastian M. Siegner
;
Laura Ugalde
;
Alexandra Clemens
;
Laura Garcia-Garcia
;
Juan A. Bueren
, et al.
소스
Nature Communications, Vol 13, Iss 1, Pp 1-15 (2022)
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7 . Academic Journal
Preclinical safety and efficacy of lentiviral-mediated gene therapy for leukocyte adhesion deficiency type I
저자
by
Cristina Mesa-Núñez
;
Carlos Damián
;
María Fernández-García
;
Begoña Díez
;
Gayatri Rao
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 459-470 (2022)
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7 . Academic Journal
Gene therapy restores the transcriptional program of hematopoietic stem cells in Fanconi anemia
저자
by
Miren Lasaga
;
Paula Río
;
Amaia Vilas-Zornoza
;
Nuria Planell
;
Susana Navarro
, et al.
소스
Haematologica, Vol 108, Iss 10 (2023)
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7 . Academic Journal
Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposes
저자
by
Julián Sevilla
;
Susana Navarro
;
Paula Rio
;
Rebeca Sánchez-Domínguez
;
Josune Zubicaray
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 22, Iss , Pp 66-75 (2021)
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7 . Academic Journal
NKG2D-CAR-transduced natural killer cells efficiently target multiple myeloma
저자
by
Alejandra Leivas
;
Antonio Valeri
;
Laura Córdoba
;
Almudena García-Ortiz
;
Alejandra Ortiz
, et al.
소스
Blood Cancer Journal, Vol 11, Iss 8, Pp 1-11 (2021)
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7 . Academic Journal
Upregulation of NKG2D ligands impairs hematopoietic stem cell function in Fanconi anemia
저자
by
José A. Casado
;
Antonio Valeri
;
Rebeca Sanchez-Domínguez
;
Paula Vela
;
Andrea López
, et al.
소스
The Journal of Clinical Investigation, Vol 132, Iss 15 (2022)
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7 . Academic Journal
Overcoming tumor resistance mechanisms in CAR-NK cell therapy
저자
by
Antonio Valeri
;
Almudena García-Ortiz
;
Eva Castellano
;
Laura Córdoba
;
Elena Maroto-Martín
, et al.
소스
Frontiers in Immunology, Vol 13 (2022)
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7 . Academic Journal
Next-generation Sequencing in Bone Marrow Failure Syndromes and Isolated Cytopenias: Experience of the Spanish Network on Bone Marrow Failure Syndromes
저자
by
Eva Gálvez
;
Elena Vallespín
;
Elena G. Arias-Salgado
;
Carmen Sánchez-Valdepeñas
;
Yari Giménez
, et al.
소스
HemaSphere, Vol 5, Iss 4, p e539 (2021)
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