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1 . Academic Journal
A novel dual-plasmid platform provides scalable transfection yielding improved productivity and packaging across multiple AAV serotypes and genomes
저자
by
Laura P. van Lieshout
;
Miranda Rubin
;
Katrina Costa-Grant
;
Stacy Ota
;
Diane Golebiowski
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 29, Iss , Pp 426-436 (2023)
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7 . Academic Journal
Natural variations in AAVHSC16 significantly reduce liver tropism and maintain broad distribution to periphery and CNS
저자
by
Laura J. Smith
;
Lindsay A. Schulman
;
Samantha Smith
;
Laura Van Lieshout
;
Carmen M. Barnes
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 26, Iss , Pp 224-238 (2022)
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7 . Academic Journal
Sustained Correction of a Murine Model of Phenylketonuria following a Single Intravenous Administration of AAVHSC15-PAH
저자
by
Seemin S. Ahmed
;
Hillard Rubin
;
Minglun Wang
;
Deiby Faulkner
;
Arnold Sengooba
, et al.
소스
Molecular Therapy: Methods & Clinical Development, Vol 17, Iss , Pp 568-580 (2020)
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7 . Academic Journal
Characterization of Impulse Oscillometric Measures of Respiratory Small Airway Function in Children
저자
by
Nancy Avila
;
Homer Nazeran
;
Erika Meraz
;
Nelly Gordillo
;
Christopher Aguilar
.
소스
Advances in Electrical and Electronic Engineering, Vol 17, Iss 1, Pp 54-63 (2019)
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7 . Academic Journal
Molecular characterization of precise in vivo targeted gene integration in human cells using AAVHSC15.
저자
by
Huei-Mei Chen
;
Rachel Resendes
;
Azita Ghodssi
;
Danielle Sookiasian
;
Michael Tian
, et al.
소스
PLoS ONE, Vol 15, Iss 5, p e0233373 (2020)
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7 . Academic Journal
Optimization of irradiation dose to Aedes aegypti and Ae. albopictus in a sterile insect technique program.
저자
by
J Guillermo Bond
;
Adriana R Osorio
;
Nancy Avila
;
Yeudiel Gómez-Simuta
;
Carlos F Marina
, et al.
소스
PLoS ONE, Vol 14, Iss 2, p e0212520 (2019)
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7 . Academic Journal
Nonclinical comparability studies of recombinant human arylsulfatase A addressing manufacturing process changes.
저자
by
Teresa Wright
;
Aiqun Li
;
Jason Lotterhand
;
Anne-Renee Graham
;
Yan Huang
, et al.
소스
PLoS ONE, Vol 13, Iss 4, p e0195186 (2018)
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7 .
Single Systemic Administration of a Gene Therapy Leading to Disease Treatment in Metachromatic LeukodystrophyArsaKnock-Out Mice
저자
by
Thia St. Martin
;
Tania A. Seabrook
;
Katherine Gall
;
Jenn Newman
;
Nancy Avila
, et al.
소스
The Journal of Neuroscience
. 43:3567-3581
Open Access (OpenAIRE)
Web of Science
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7 .
Gene therapy for metachromatic leukodystrophy: Lead candidate optimization
저자
by
Jacinthe Gingras
;
Thia St Martin
;
Katie Gall
;
Jennifer Newman
;
Donald E. Selby
, et al.
소스
Molecular Genetics and Metabolism
. 138:107112
Web of Science
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7 .
Sustained Correction of a Murine Model of Phenylketonuria following a Single Intravenous Administration of AAVHSC15-PAH
저자
by
Minglun Wang
;
Hillard Rubin
;
Jason Lotterhand
;
Omar L. Francone
;
Maria Lobikin
, et al.
소스
Molecular Therapy. Methods & Clinical Development
Molecular Therapy: Methods & Clinical Development, Vol 17, Iss, Pp 568-580 (2020)
Open Access (OpenAIRE)
Scopus
JCR 저널정보
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