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1 . Academic Journal
MD-1 downregulation is associated with reduced cell surface CD180 expression in CLL
저자
by
Edwards, Kurtis
;
Manoussaka, Maria
;
Sayed, Uzma
;
Tsertsvadze, Tamar
;
Deyn, Lara De
, et al.
소스
In
Leukemia Research
August 2024 143
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7 . Academic Journal
Illustrated State‐of‐the‐Art Capsules of the ISTH 2019 Congress in Melbourne, Australia
저자
by
Ward, Christopher M.
;
Andrews, Robert K.
;
Barco, Stefano
;
Battinelli, E.M.
;
Boilard, Eric
, et al.
소스
In
Research and Practice in Thrombosis and Haemostasis
July 2019 3(3):431-497
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7 . Academic Journal
A high-throughput sequencing test for diagnosing inherited bleeding, thrombotic, and platelet disorders
저자
by
Simeoni, Ilenia
;
Stephens, Jonathan C.
;
Hu, Fengyuan
;
Deevi, Sri V.V.
;
Megy, Karyn
, et al.
소스
In
Blood
9 June 2016 127(23):2791-2803
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7 . Academic Journal
Nebulized Recombinant Tissue Plasminogen Activator (rt-PA) for Acute COVID-19-Induced Respiratory Failure: An Exploratory Proof-of-Concept Trial.
저자
by
Chowdary, Pratima
;
Agarwal, Banwari
;
Peralta, Maria Rita
;
Bhagani, Sanjay
;
Lee, Simon
, et al.
소스
Journal of Clinical Medicine
. Sep2023, Vol. 12 Issue 18, p5848. 17p.
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7 . Academic Journal
Adeno-associated virus gene therapy prevents progression of kidney disease in genetic models of nephrotic syndrome.
저자
by
Ding, Wen Y.
;
Kuzmuk, Valeryia
;
Hunter, Sarah
;
Lay, Abigail
;
Hayes, Bryony
, et al.
소스
Science Translational Medicine; 8/9/2023, Vol. 15 Issue 708, p1-17, 17p
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7 . Academic Journal
The Effect of In Vivo T Cell Depletion with Alemtuzumab on Reduced-Intensity Allogeneic Hematopoietic Cell Transplantation for Chronic Lymphocytic Leukemia
저자
by
Delgado, Julio
;
Pillai, Srinivas
;
Benjamin, Reuben
;
Caballero, Dolores
;
Martino, Rodrigo
, et al.
소스
In
Biology of Blood and Marrow Transplantation
2008 14(11):1288-1297
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7 . Periodical
Preclinical evaluation of FLT190, a liver-directed AAV gene therapy for Fabry disease
저자
by
Jeyakumar, Jey M.
;
Kia, Azadeh
;
Tam, Lawrence C. S.
;
McIntosh, Jenny
;
Spiewak, Justyna
, et al.
소스
Gene Therapy; June 2023, Vol. 30 Issue: 6 p487-502, 16p
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7 . Academic Journal
Phase 1-2 Trial of AAVS3 Gene Therapy in Patients with Hemophilia B.
저자
by
Chowdary, Pratima
;
Shapiro, Susan
;
Makris, Mike
;
Evans, Gillian
;
Boyce, Sara
, et al.
소스
New England Journal of Medicine
. 7/21/2022, Vol. 387 Issue 3, p237-247. 11p.
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7 . Academic Journal
Factor IX Expression within the Normal Range Prevents Spontaneous Bleeds Requiring Treatment Following FLT180a Gene Therapy in Patients with Severe Hemophilia B: Long-Term Follow-up Study of the B-Amaze Program
저자
by
Chowdary, Pratima
;
Shapiro, Susan
;
Makris, Mike
;
Evans, Gillian
;
Boyce, Sara
, et al.
소스
In
Blood
23 November 2021 138 Supplement 1:3967-3967
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7 . Academic Journal
Highly efficient gene transfer into cord blood nonobese diabetic/severe combined immunodeficiency repopulating cells by oncoretroviral vector particles pseudotyped with the feline endogenous retrovirus (RD114) envelope protein
저자
by
Kelly, Patrick F.
;
Vandergriff, Jody
;
Nathwani, Amit
;
Nienhuis, Arthur W.
;
Vanin, Elio F.
.
소스
In
Blood
15 August 2000 96(4):1206-1214
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