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1 . Academic Journal
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
저자
by
Bersani, Margherita
;
Rizzuti, Mafalda
;
Pagliari, Elisa
;
Garbellini, Manuela
;
Saccomanno, Domenica
, et al.
소스
In
Molecular Therapy
2 March 2022 30(3):1288-1299
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7 . Academic Journal
Hexose Potentiates Peptide-Conjugated Morpholino Oligomer Efficacy in Cardiac Muscles of Dystrophic Mice in an Age-Dependent Manner
저자
by
Han, Gang
;
Gu, Ben
;
Lin, Caorui
;
Ning, Hanhan
;
Song, Jun
, et al.
소스
In
Molecular Therapy - Nucleic Acids
6 December 2019 18:341-350
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7 . Academic Journal
ACE2 acts as a novel regulator of TMPRSS2-catalyzed proteolytic activation of influenza A virus in airway cells.
저자
by
Heindl, Miriam Ruth
;
Rupp, Anna-Lena
;
Schwerdtner, Marie
;
Bestle, Dorothea
;
Harbig, Anne
, et al.
소스
Journal of Virology
. Apr2024, Vol. 98 Issue 4, p1-20. 20p.
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7 . Academic Journal
Effect of Combined Systemic and Local Morpholino Treatment on the Spinal Muscular Atrophy Δ7 Mouse Model Phenotype
저자
by
Nizzardo, Monica
;
Simone, Chiara
;
Salani, Sabrina
;
Ruepp, Marc-David
;
Rizzo, Federica
, et al.
소스
In
Clinical Therapeutics
1 March 2014 36(3):340-356
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7 . Academic Journal
Long-Term Rescue of Dystrophin Expression and Improvement in Muscle Pathology and Function in Dystrophic mdx Mice by Peptide-Conjugated Morpholino
저자
by
Wu, Bo
;
Lu, Peijuan
;
Cloer, Caryn
;
Shaban, Mona
;
Grewal, Snimar
, et al.
소스
In
The American Journal of Pathology
August 2012 181(2):392-400
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7 . Academic Journal
Fructose Promotes Uptake and Activity of Oligonucleotides with Different Chemistries in a Context-Dependent Manner in mdx Mice
저자
by
Cao, Limin
;
Han, Gang
;
Lin, Caorui
;
Gu, Ben
;
Gao, Xianjun
, et al.
소스
In
Molecular Therapy - Nucleic Acids
4 December 2020 22:1040-1042
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7 . Academic Journal
Cell penetrating peptide conjugates of steric block oligonucleotides
저자
by
Lebleu, Bernard
;
Moulton, Hong M.
;
Abes, Rachida
;
Ivanova, Gabriela D.
;
Abes, Said
, et al.
소스
In
Advanced Drug Delivery Reviews
2008 60(4):517-529
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7 . Academic Journal
Inhibition of replication and transcription activator and latency-associated nuclear antigen of Kaposi's sarcoma-associated herpesvirus by morpholino oligomers
저자
by
Zhang, Yan-Jin
;
Wang, Kai-Yu
;
Stein, David A.
;
Patel, Deendayal
;
Watkins, Rheba
, et al.
소스
In
Antiviral Research
January 2007 73(1):12-23
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7 . Academic Journal
Vectorization of morpholino oligomers by the (R-Ahx-R) 4 peptide allows efficient splicing correction in the absence of endosomolytic agents
저자
by
Abes, Saïd
;
Moulton, Hong M.
;
Clair, Philippe
;
Prevot, Paul
;
Youngblood, Derek S.
, et al.
소스
In
Journal of Controlled Release
2006 116(3):304-313
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7 . Academic Journal
Development of DG9 peptide-conjugated single- and multi-exon skipping therapies for the treatment of Duchenne muscular dystrophy.
저자
by
Lim, Kenji Rowel Q.
;
Woo, Stanley
;
Melo, Dyanna
;
Huang, Yiqing
;
Dzierlega, Kasia
, et al.
소스
Proceedings of the National Academy of Sciences of the United States of America
. 3/1/2022, Vol. 119 Issue 9, p1-7. 19p.
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