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1 . Academic Journal
Practical Considerations for Delandistrogene Moxeparvovec Gene Therapy in Patients With Duchenne Muscular Dystrophy
저자
by
Mendell, Jerry R.
;
Proud, Crystal
;
Zaidman, Craig M.
;
Mason, Stefanie
;
Darton, Eddie
, et al.
소스
In
Pediatric Neurology
April 2024 153:11-18
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7 . Academic Journal
Influence of β2 adrenergic receptor genotype on longitudinal measures of forced vital capacity in patients with Duchenne muscular dystrophy
저자
by
Kelley, Eli F
;
Cross, Troy J
;
McDonald, Craig M.
;
Hoffman, Eric P.
;
Bello, Luca
.
소스
In
Neuromuscular Disorders
February 2022 32(2):150-158
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7 . Academic Journal
Health related quality of life in young, steroid-naïve boys with Duchenne muscular dystrophy
저자
by
Straub, Volker
;
Childs, Anne-Marie
;
Ciafaloni, Emma
;
Shieh, Perry B.
;
Spinty, Stefan
, et al.
소스
In
Neuromuscular Disorders
November 2021 31(11):1161-1168
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7 . Academic Journal
Rasch Analysis of the Pediatric Quality of Life Inventory 4.0 Generic Core Scales Administered to Patients With Duchenne Muscular Dystrophy
저자
by
Vishwanathan, V.
;
Chidambaranathan, S.
;
Biggar, W. Douglas
;
McAdam, Laura C.
;
Mah, Jean K.
, et al.
소스
In
Value in Health
October 2021 24(10):1490-1498
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7 . Report
Gait Event Detection and Travel Distance Using Waist-Worn Accelerometers across a Range of Speeds: Automated Approach
저자
by
Ramli, Albara Ah
;
Liu, Xin
;
Berndt, Kelly
;
Chuah, Chen-Nee
;
Goude, Erica
, et al.
소스
Sensors. 2024; 24(4):1155
Open Access (Arxiv)
Find it @ DONGA
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7 . Academic Journal
Survival among patients receiving eteplirsen for up to 8 years for the treatment of Duchenne muscular dystrophy and contextualization with natural history controls.
저자
by
Iff, Joel
;
Done, Nicolae
;
Tuttle, Edward
;
Zhong, Yi
;
Wei, Fangzhou
, et al.
소스
Muscle & Nerve
. Jul2024, Vol. 70 Issue 1, p60-70. 11p.
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7 . Academic Journal
Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study
저자
by
Vishwanathan, Vijay
;
Chidambaranathan, S
;
Biggar, W. Douglas
;
McAdam, Laura C.
;
Mah, Jean K.
, et al.
소스
In
The Lancet
3-9 February 2018 391(10119):451-461
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7 . Academic Journal
Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials.
저자
by
McDonald, Craig M.
;
Signorovitch, James
;
Mercuri, Eugenio
;
Niks, Erik H.
;
Wong, Brenda
, et al.
소스
PLoS ONE
. 6/3/2024, Vol. 19 Issue 6, p1-20. 20p.
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7 . Academic Journal
Idebenone reduces respiratory complications in patients with Duchenne muscular dystrophy
저자
by
Bernert, G.
;
Knipp, F.
;
Buyse, G.M.
;
Goemans, N.
;
van den Hauwe, M.
, et al.
소스
In
Neuromuscular Disorders
August 2016 26(8):473-480
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7 . Academic Journal
Evaluation of Phrenic Nerve and Diaphragm Function with Peripheral Nerve Stimulation and M-Mode Ultrasonography in Potential Pediatric Phrenic Nerve or Diaphragm Pacing Candidates
저자
by
Skalsky, Andrew J.
;
Lesser, Daniel J.
;
McDonald, Craig M.
.
소스
In
Physical Medicine & Rehabilitation Clinics of North America
February 2015 26(1):133-143
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