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1 . Academic Journal
Novel lentiviral vectors for gene therapy of sickle cell disease combining gene addition and gene silencing strategies
저자
by
Mégane Brusson
;
Anne Chalumeau
;
Pierre Martinucci
;
Oriana Romano
;
Tristan Felix
, et al.
소스
Molecular Therapy: Nucleic Acids, Vol 32, Iss , Pp 229-246 (2023)
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7 . Academic Journal
Base-editing-mediated dissection of a γ-globin cis-regulatory element for the therapeutic reactivation of fetal hemoglobin expression
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by
Panagiotis Antoniou
;
Giulia Hardouin
;
Pierre Martinucci
;
Giacomo Frati
;
Tristan Felix
, et al.
소스
Nature Communications, Vol 13, Iss 1, Pp 1-22 (2022)
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7 . Academic Journal
Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins
저자
by
Giulia Pavani
;
Marine Laurent
;
Anna Fabiano
;
Erika Cantelli
;
Aboud Sakkal
, et al.
소스
Nature Communications, Vol 11, Iss 1, Pp 1-13 (2020)
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7 . Academic Journal
Corrigendum: Targeted Gene Delivery: Where to Land
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by
Giulia Pavani
;
Mario Amendola
.
소스
Frontiers in Genome Editing, Vol 3 (2021)
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4 . Academic Journal
Targeted Gene Delivery: Where to Land
저자
by
Giulia Pavani
;
Mario Amendola
.
소스
Frontiers in Genome Editing, Vol 2 (2021)
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4 . Academic Journal
GATA Factor-Mediated Gene Regulation in Human Erythropoiesis
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by
Oriana Romano
;
Luca Petiti
;
Tristan Felix
;
Vasco Meneghini
;
Michel Portafax
, et al.
소스
iScience, Vol 23, Iss 4, Pp - (2020)
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7 . Academic Journal
Author Correction: Ex vivo editing of human hematopoietic stem cells for erythroid expression of therapeutic proteins
저자
by
Giulia Pavani
;
Marine Laurent
;
Anna Fabiano
;
Erika Cantelli
;
Aboud Sakkal
, et al.
소스
Nature Communications, Vol 11, Iss 1, Pp 1-1 (2020)
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7 . Academic Journal
Oxidative stress and cell death in cells expressing L-ferritin variants causing neuroferritinopathy
저자
by
Anna Cozzi
;
Elisabetta Rovelli
;
Grazia Frizzale
;
Alessandro Campanella
;
Mario Amendola
, et al.
소스
Neurobiology of Disease, Vol 37, Iss 1, Pp 77-85 (2010)
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7 .
CRISPR-Cas9 mediated endogenous utrophin upregulation improves Duchenne Muscular Dystrophy
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by
Simon Guiraud
;
Sumitava Dastidar
;
Fetta Mazed
;
Fatima Amor
;
Maelle Ralu
, et al.
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7 .
Supplementary Methods, Figures 1-3 from Reprogramming T Lymphocytes for Melanoma Adoptive Immunotherapy by T-Cell Receptor Gene Transfer with Lentiviral Vectors
저자
by
Antonio Rosato
;
Paola Zanovello
;
Reno Debets
;
Ralph A. Willemsen
;
Luigi Naldini
, et al.
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