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1 . Academic Journal
Onasemnogene abeparvovec in spinal muscular atrophy: predictors of efficacy and safety in naïve patients with spinal muscular atrophy and following switch from other therapiesResearch in context
저자
by
Marika Pane
;
Beatrice Berti
;
Anna Capasso
;
Giorgia Coratti
;
Antonio Varone
, et al.
소스
EClinicalMedicine, Vol 59, Iss , Pp 101997- (2023)
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7 . Academic Journal
Nusinersen efficacy data for 24‐month in type 2 and 3 spinal muscular atrophy
저자
by
Marika Pane
;
Giorgia Coratti
;
Maria Carmela Pera
;
Valeria A. Sansone
;
Sonia Messina
, et al.
소스
Annals of Clinical and Translational Neurology, Vol 9, Iss 3, Pp 404-409 (2022)
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7 . Academic Journal
Nusinersen in pediatric and adult patients with type III spinal muscular atrophy
저자
by
Maria Carmela Pera
;
Giorgia Coratti
;
Francesca Bovis
;
Marika Pane
;
Amy Pasternak
, et al.
소스
Annals of Clinical and Translational Neurology, Vol 8, Iss 8, Pp 1622-1634 (2021)
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7 . Academic Journal
Type I SMA 'new natural history': long‐term data in nusinersen‐treated patients
저자
by
Marika Pane
;
Giorgia Coratti
;
Valeria A. Sansone
;
Sonia Messina
;
Michela Catteruccia
, et al.
소스
Annals of Clinical and Translational Neurology, Vol 8, Iss 3, Pp 548-557 (2021)
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7 . Academic Journal
Diagnostic journey in Spinal Muscular Atrophy: Is it still an odyssey?
저자
by
Maria Carmela Pera
;
Giorgia Coratti
;
Beatrice Berti
;
Adele D'Amico
;
Maria Sframeli
, et al.
소스
PLoS ONE, Vol 15, Iss 3, p e0230677 (2020)
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7 . Academic Journal
Nusinersen Modulates Proteomics Profiles of Cerebrospinal Fluid in Spinal Muscular Atrophy Type 1 Patients
저자
by
Laura Bianchi
;
Maria Sframeli
;
Lorenza Vantaggiato
;
Gian Luca Vita
;
Annamaria Ciranni
, et al.
소스
International Journal of Molecular Sciences, Vol 22, Iss 9, p 4329 (2021)
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7 . Academic Journal
A Phase 1/2 Study of Flavocoxid, an Oral NF-κB Inhibitor, in Duchenne Muscular Dystrophy
저자
by
Gian Luca Vita
;
Maria Sframeli
;
Norma Licata
;
Alessandra Bitto
;
Sara Romeo
, et al.
소스
Brain Sciences, Vol 11, Iss 1, p 115 (2021)
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7 . Academic Journal
New Treatments in Spinal Muscular Atrophy: Positive Results and New Challenges
저자
by
Sonia Messina
;
Maria Sframeli
.
소스
Journal of Clinical Medicine, Vol 9, Iss 7, p 2222 (2020)
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4 .
Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled trial
저자
by
Eugenio Mercuri
;
Nicolas Deconinck
;
Elena S Mazzone
;
Andres Nascimento
;
Maryam Oskoui
, et al.
소스
LANCET NEUROLOGY
r-FSJD. Repositorio Institucional de Producción Científica de la Fundació Sant Joan de Déu
instname
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7 .
Reworsening of Recurrent Guillain-Barré Syndrome Triggered by COVID-19 Infection
저자
by
Maria Sframeli
;
Giuseppe Vita
;
Carmen Terranova
;
Antonio Toscano
;
Gian Luca Vita
.
소스
The Open Neurology Journal
. 15:48-51
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