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1 . Academic Journal
Therapeutic Approaches in Facioscapulohumeral Muscular Dystrophy
저자
by
Cohen, Justin
;
DeSimone, Alec
;
Lek, Monkol
;
Lek, Angela
.
소스
In
Trends in Molecular Medicine
February 2021 27(2):123-137
Full Text (ScienceDirect)
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6 . Periodical
Meeting Report: 2023 Muscular Dystrophy Association Summit on ‘Safety and Challenges in Gene Therapy of Neuromuscular Diseases’
저자
by
Lek, Angela
;
Atas, Evrim
;
Lin, Brian
;
Hesterlee, Sharon E.
;
Abbott, Jordan K.
, et al.
소스
Journal of Neuromuscular Diseases; September 2024, Vol. 11 Issue: 5 p1139-1160, 22p
Web of Science
Scopus
Find it @ DONGA
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7 . Academic Journal
Emerging preclinical animal models for FSHD
저자
by
Lek, Angela
;
Rahimov, Fedik
;
Jones, Peter L.
;
Kunkel, Louis M.
.
소스
In
Trends in Molecular Medicine
May 2015 21(5):295-306
Full Text (ScienceDirect)
Full Text (Clinical Key)
Web of Science
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JCR 저널정보
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6 . Academic Journal
Profilin1 is required for prevention of mitotic catastrophe in murine and human glomerular diseases.
저자
by
Xuefei Tian
;
Pedigo, Christopher E.
;
Ke Li
;
Xiaotao Ma
;
Bunda, Patricia
, et al.
소스
Journal of Clinical Investigation
. 12/15/2023, Vol. 133 Issue 24, p1-18. 18p.
Web of Science
Scopus
JCR 저널정보
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7 . Academic Journal
Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne's Muscular Dystrophy.
저자
by
Lek, Angela
;
Keeler, Allison
;
Flotte, Terence R.
.
소스
New England Journal of Medicine
. 12/7/2023, Vol. 389 Issue 23, p2211-2211. 13p.
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5 . Academic Journal
Development of Assays to Measure GNE Gene Potency and Gene Replacement in Skeletal Muscle.
저자
by
Zygmunt, Deborah A.
;
Lam, Patricia
;
Ashbrook, Anna
;
Koczwara, Katherine
;
Lek, Angela
, et al.
소스
Journal of Neuromuscular Diseases; 2023, Vol. 10 Issue 5, p797-812, 16p
Web of Science
Scopus
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7 . Periodical
The Muscular Dystrophy Association’s neuroMuscular ObserVational Research Data Hub (MOVR): Design, Methods, and Initial Observations
저자
by
Kilroy, Elisabeth A
;
Burris, Rachael
;
Javelosa, Edritz
;
Waits, Jessica
;
Lek, Angela
, et al.
소스
Journal of Neuromuscular Diseases; November 2023, Vol. 10 Issue: 3 p365-380, 16p
Web of Science
Scopus
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7 . Academic Journal
Meeting Report: 2022 Muscular Dystrophy Association Summit on 'Safety and Challenges in Gene Transfer Therapy'.
저자
by
Lek, Angela
;
Atas, Evrim
;
Hesterlee, Sharon E.
;
Byrne, Barry J.
;
Bönnemann, Carsten G.
.
소스
Journal of Neuromuscular Diseases; 2023, Vol. 10 Issue 3, p327-336, 10p
Web of Science
Scopus
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7 . Periodical
Development of Assays to Measure GNEGene Potency and Gene Replacement in Skeletal Muscle
저자
by
Zygmunt, Deborah A.
;
Lam, Patricia
;
Ashbrook, Anna
;
Koczwara, Katherine
;
Lek, Angela
, et al.
소스
Journal of Neuromuscular Diseases; September 2023, Vol. 10 Issue: 5 p797-812, 16p
Web of Science
Scopus
Find it @ DONGA
요약보기
Export
E-Mail
EndNote
RefWorks
7 . Academic Journal
Nuclease-Deficient Clustered Regularly Interspaced Short Palindromic Repeat-Based Approaches for In Vitro and In Vivo Gene Activation.
저자
by
Lek, Angela
;
Ma, Kaiyue
;
Woodman, Keryn G.
;
Lek, Monkol
.
소스
Human Gene Therapy
. Mar2021, Vol. 23 Issue 5/6, p260-274. 15p.
Web of Science
Scopus
JCR 저널정보
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