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1 . Academic Journal
Eradication of neutralizing antibodies to factor VIII in canine hemophilia A after liver gene therapy
저자
by
Finn, Jonathan D.
;
Ozelo, Margareth C.
;
Sabatino, Denise E.
;
Franck, Helen W.G.
;
Merricks, Elizabeth P.
, et al.
소스
In
Blood
23 December 2010 116(26):5842-5848
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7 . Academic Journal
Phenotypic correction of a mouse model of hemophilia A using AAV2 vectors encoding the heavy and light chains of FVIII
저자
by
Scallan, Ciaran D.
;
Liu, Tongyao
;
Parker, Amy E.
;
Patarroyo-White, Susannah L.
;
Chen, Haifeng
, et al.
소스
In
Blood
1 December 2003 102(12):3919-3926
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7 . Academic Journal
Reflections on the history of genetic medicine at Johns Hopkins University.
저자
by
Migeon, Barbara R.
;
Kazazian, Haig H.
.
소스
American Journal of Medical Genetics. Part A; Nov2021, Vol. 185 Issue 11, p3224-3229, 6p
Web of Science
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4 . Academic Journal
A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells.
저자
by
Nguyen, Giang N.
;
Everett, John K.
;
Kafle, Samita
;
Roche, Aoife M.
;
Raymond, Hayley E.
, et al.
소스
Nature Biotechnology; 2021, Vol. 39 Issue 1, p47-55, 9p
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7 . Academic Journal
Author Correction: Pan-cancer analysis of whole genomes identifies driver rearrangements promoted by LINE-1 retrotransposition
저자
by
Rodriguez-Martin, Bernardo
;
Alvarez, Eva G.
;
Baez-Ortega, Adrian
;
Zamora, Jorge
;
Supek, Fran
, et al.
소스
Nature Genetics
. 55(6):1080-1080
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7 . Periodical
Pan-cancer analysis of whole genomes identifies driver rearrangements promoted by LINE-1 retrotransposition
저자
by
Rodriguez-Martin, Bernardo
;
Alvarez, Eva G.
;
Baez-Ortega, Adrian
;
Zamora, Jorge
;
Supek, Fran
, et al.
소스
Nature Genetics; March 2020, Vol. 52 Issue: 3 p306-319, 14p
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7 . Academic Journal
Reading LINEs within the cocaine addicted brain.
저자
by
Doyle, Glenn A.
;
Doucet ‐ O'Hare, Tara T.
;
Hammond, Matthew J.
;
Crist, Richard C.
;
Ewing, Adam D.
, et al.
소스
Brain & Behavior
. May2017, Vol. 7 Issue 5, pn/a-N.PAG. 12p.
Open Access (Wiley)
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7 . Academic Journal
Somatically Acquired LINE-1 Insertions in Normal Esophagus Undergo Clonal Expansion in Esophageal Squamous Cell Carcinoma.
저자
by
Doucet‐O'Hare, Tara T.
;
Sharma, Reema
;
Rodić, Nemanja
;
Anders, Robert A.
;
Burns, Kathleen H.
, et al.
소스
Human Mutation; Sep2016, Vol. 37 Issue 9, p943-954, 13p
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7 . Academic Journal
A long-term study of AAV gene therapy in dogs with hemophilia A identifies clonal expansions of transduced liver cells
저자
by
Nguyen, Giang N.
;
Everett, John K.
;
Kafle, Samita
;
Roche, Aoife M.
;
Raymond, Hayley E.
, et al.
소스
NATURE BIOTECHNOLOGY
; NOV 16 2020, 16p.
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7 . Academic Journal
25 Years of Human Mutation
저자
by
Cutting, Garry R.
;
Kazazian, Haig H., Jr.
.
소스
Human Mutation
. Jun 01, 2016 37(6):503-504
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