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1 . Academic Journal
Patient and caregiver perspectives on guideline adherence: the case of endocrine and bone health recommendations for Duchenne muscular dystrophy
저자
by
Brian Denger
;
Kathi Kinnett
;
Ann Martin
;
Sean Grant
;
Courtney Armstrong
, et al.
소스
Orphanet Journal of Rare Diseases, Vol 14, Iss 1, Pp 1-10 (2019)
Open Access (BioMed Central)
Open Access (DOAJ)
Web of Science
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7 . Academic Journal
Current state of cardiac troponin testing in Duchenne muscular dystrophy cardiomyopathy: review and recommendations from the Parent Project Muscular Dystrophy expert panel
저자
by
Christopher F Spurney
;
Lawrence Charnas
;
Linda Cripe
;
Kan Hor
;
Nicholas King
, et al.
소스
Open Heart, Vol 8, Iss 1 (2021)
Open Access (DOAJ)
Scopus
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7 .
Dystrophinopathy and the brain: A parent project muscular dystrophy (PPMD) meeting report November 11-12, 2021, New York City, NY
저자
by
Mary K. Colvin
;
Natalie Truba
;
Seth Sorensen
;
Erik Henricson
;
Kathi Kinnett
.
소스
Neuromuscular Disorders
. 32:935-944
Full Text (Clinical Key)
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7 .
Current Practices in Treating Cardiomyopathy and Heart Failure in Duchenne Muscular Dystrophy (DMD): Understanding Care Practices in Order to Optimize DMD Heart Failure Through ACTION
저자
by
Chet Villa
;
Scott R. Auerbach
;
Neha Bansal
;
Brian F. Birnbaum
;
Jennifer Conway
, et al.
소스
Pediatric Cardiology
Open Access (OpenAIRE)
Web of Science
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7 .
Parent Project Muscular Dystrophy Females with Dystrophinopathy Conference, Orlando, Florida June 26 – June 27, 2019
저자
by
Brenda L. Wong
;
May Ling Mah
;
Joe N. Kornegay
;
Jamie L. Jackson
;
Dongsheng Duan
, et al.
소스
Journal of Neuromuscular Diseases
. 8:315-322
Web of Science
Scopus
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7 .
Role Attainment in Emerging Adulthood: Subjective Evaluation by Male Adolescents and Adults with Duchenne and Becker Muscular Dystrophy
저자
by
Holly L. Peay
;
Barbara T. Do
;
Neil Khosla
;
Pangaja Paramsothy
;
Stephen W. Erickson
, et al.
소스
J Neuromuscul Dis
Open Access (OpenAIRE)
Scopus
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7 .
Using an Online, Modified Delphi Approach to Engage Patients and Caregivers in Determining the Patient-Centeredness of Duchenne Muscular Dystrophy Care Considerations
저자
by
Holly L. Peay
;
Christine Chen
;
Sean Grant
;
Glen Hazlewood
;
Natalie Street
, et al.
소스
Medical Decision Making
Open Access (OpenAIRE)
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7 .
Practical Considerations in Using Online Modified-Delphi Approaches to Engage Patients and Other Stakeholders in Clinical Practice Guideline Development
저자
by
Holly L. Peay
;
Ian D. Coulter
;
Sean Grant
;
Kathi Kinnett
;
Ann Martin
, et al.
소스
The Patient
Open Access (OpenAIRE)
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7 .
Unique Burdens of Pediatric Clinical Trials in Duchenne Muscular Dystrophy, April 20–21, 2017, Bethesda, Maryland, USA
저자
by
Kathi Kinnett
;
Timothy P. Cripe
;
Timothy Franson
.
소스
Therapeutic Innovation & Regulatory Science
. 53:154-163
Web of Science
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5 .
Management of Adrenal Insufficiency Risk After Long-term Systemic Glucocorticoid Therapy in Duchenne Muscular Dystrophy: Clinical Practice Recommendations
저자
by
Kathi Kinnett
;
Sasigarn A. Bowden
;
Philip Zeitler
;
Anne M. Connolly
.
소스
Journal of Neuromuscular Diseases
Open Access (OpenAIRE)
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