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1 . Academic Journal
Recommendations for a minimum data set for monitoring gene therapy in hemophilia: communication from the ISTH SSC Working Group on Gene Therapy
저자
by
Miesbach, Wolfgang
;
Konkle, Barbara
;
Chowdary, Pratima
;
Kaczmarek, Radoslaw
;
Leebeek, Frank
, et al.
소스
In
Journal of Thrombosis and Haemostasis
May 2024 22(5):1510-1515
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7 . Academic Journal
Deciphering conundrums of adeno-associated virus liver-directed gene therapy: focus on hemophilia
저자
by
Pierce, Glenn F.
;
Fong, Sylvia
;
Long, Brian R.
;
Kaczmarek, Radoslaw
.
소스
In
Journal of Thrombosis and Haemostasis
May 2024 22(5):1263-1289
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6 . Academic Journal
Optimizing liver health before and after gene therapy for hemophilia A
저자
by
Ragni, Margaret V.
;
Mead, Henry
;
de Jong, Ype P.
;
Kaczmarek, Radoslaw
;
Leavitt, Andrew D.
, et al.
소스
In
Blood Advances
May 2024
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7 . Academic Journal
Factor IX administration in the skin primes inhibitor formation and sensitizes hemophilia B mice to systemic factor IX administration
저자
by
Sherman, Alexandra
;
Bertolini, Thais B.
;
Arisa, Sreevani
;
Herzog, Roland W.
;
Kaczmarek, Radoslaw
.
소스
In
Research and Practice in Thrombosis and Haemostasis
November 2023 7(8)
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7 . Academic Journal
Hemophilia gene therapy: first, do no harm
저자
by
Valentino, Leonard A.
;
Kaczmarek, Radoslaw
;
Pierce, Glenn F.
;
Noone, Declan
;
O’Mahony, Brian
, et al.
소스
In
Journal of Thrombosis and Haemostasis
September 2023 21(9):2354-2361
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7 . Academic Journal
Factor VIII trafficking to CD4+ T cells shapes its immunogenicity and requires several types of antigen-presenting cells
저자
by
Kaczmarek, Radoslaw
;
Piñeros, Annie R.
;
Patterson, Paige E.
;
Bertolini, Thais B.
;
Perrin, George Q.
, et al.
소스
In
Blood
20 July 2023 142(3):290-305
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7 . Academic Journal
Density results and trace operator in weighted Sobolev spaces defined on the half-line, equipped with power weights
저자
by
Kaczmarek, Radosław
;
Kałamajska, Agnieszka
.
소스
In
Journal of Approximation Theory
July 2023 291
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4 . Academic Journal
Achieving access to haemophilia care in low-income and lower-middle-income countries: expanded Humanitarian Aid Program of the World Federation of Hemophilia after 5 years
저자
by
Pierce, Glenn F
;
Adediran, Megan
;
Diop, Saliou
;
Dunn, Amy L
;
El Ekiaby, Magdy
, et al.
소스
In
The Lancet Haematology
September 2022 9(9):e689-e697
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7 . Academic Journal
Risk of harm to people with haemophilia from the 2023 WHO Essential Medicines List
저자
by
Crato, Miguel
;
Dunn, Amy
;
Gouider, Emna
;
Mahlangu, Johnny
;
Page, David
, et al.
소스
In
The Lancet Haematology
September 2024 11(9):e638-e640
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7 . Academic Journal
Sudden Vision Loss as the First Sign of Sepsis—Bilateral Endogenous Endophthalmitis of Uncommon Capnocytophaga canimorsus Etiology.
저자
by
Łątkowska, Małgorzata
;
Gajdzis, Małgorzata
;
Turno-Kręcicka, Anna
;
Kręcicka, Julia
;
Mimier-Janczak, Małgorzata
, et al.
소스
Medicina (1010660X); Jun2024, Vol. 60 Issue 6, p896, 6p
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